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Progressive neurodegeneration, motor decline, and premature mortality in aging Ngly1 deficient rats

Lei Zhu1,2, Selina Dwight1,2, William F Mueller3,4

  • 1Grace Science, LLC, Menlo Park, CA, 94025, USA.

Orphanet Journal of Rare Diseases
|February 20, 2026
PubMed
Abstract

No abstract available in PubMed .

Keywords:
CNSMortalityMotor functionNGLY1NGLY1 DeficiencyRare diseases

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