Evaluating effects of risdiplam in adults with spinal muscular atrophy: a monocentric study

Grazia Crescimanno1,2, Paolo Alonge2, Antonino Lupica2

  • 1National Research Council, Institute of Biomedical Research and Innovation (IRIB-CNR), Palermo, Italy.

ERJ Open Research
|March 18, 2026
PubMed