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Updated: Jun 30, 2026

CRISPR/Cas9-mediated Targeted Integration In Vivo Using a Homology-mediated End Joining-based Strategy
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Modest rescue of RBFOX1 splicing function attenuates Huntington's disease features

David Lozano-Muñoz1,2, Ainara Elorza1,2, Miriam Lucas-Santamaría1,2

  • 1Center for Molecular Biology Severo Ochoa (CBM Severo Ochoa) CSIC/UAM, C/ Nicolás Cabrera, 1, Madrid, 28049, Spain.

Molecular Medicine (Cambridge, Mass.)
|April 3, 2026
PubMed
Summary

No abstract available in PubMed .

Keywords:
A2BP1Huntington´s diseaseRBFOXSplicingTransgenic mice

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