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Updated: Apr 22, 2026

Ole Isacson: Development of New Therapies for Parkinson's Disease
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Current and emerging therapeutic advancements for Niemann-Pick disease type C: where are we now and what does the

Andreas Hahn1

  • 1Department of Pediatric Neurology and Center of Rare Diseases, Justus-Liebig-University, Giessen, Germany.

Expert Review of Neurotherapeutics
|April 20, 2026
PubMed
Abstract

Keywords:
Lysosomal storage diseaseNPC1NPC2Niemann-Pick-disease type Carimoclomolcyclodextrinlevoacetylleucinemiglustat

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