Related Experiment Video

Updated: Apr 24, 2026

Efficient Gene Knockdown in the Liver via Intrasplenic Injection of Adeno-Associated Virus Serotype 8 (AAV8)-Delivered Small Hairpin RNA
04:29

Efficient Gene Knockdown in the Liver via Intrasplenic Injection of Adeno-Associated Virus Serotype 8 (AAV8)-Delivered Small Hairpin RNA

Published on: November 1, 2024

1.1K

Response to hemophilia B gene therapy based on adenoassociated virus serotype 5 antibody status

Wolfgang Miesbach1, Alok Srivastava2

  • 1Medical Clinic 2, University Hospital Frankfurt, Frankfurt, Germany.

Research and Practice in Thrombosis and Haemostasis
|April 23, 2026
PubMed
Abstract

No abstract available in PubMed .

More Related Videos

A Step-By-Step Method to Detect Neutralizing Antibodies Against AAV using a Colorimetric Cell-Based Assay
05:53

A Step-By-Step Method to Detect Neutralizing Antibodies Against AAV using a Colorimetric Cell-Based Assay

Published on: December 7, 2021

4.4K
Author Spotlight: Optimizing Digital Droplet PCR Method for Accurate Adeno-Associated Viral Genome Quantification
04:43

Author Spotlight: Optimizing Digital Droplet PCR Method for Accurate Adeno-Associated Viral Genome Quantification

Published on: October 11, 2024

2.2K

Related Experiment Videos

Last Updated: Apr 24, 2026

Efficient Gene Knockdown in the Liver via Intrasplenic Injection of Adeno-Associated Virus Serotype 8 (AAV8)-Delivered Small Hairpin RNA
04:29

Efficient Gene Knockdown in the Liver via Intrasplenic Injection of Adeno-Associated Virus Serotype 8 (AAV8)-Delivered Small Hairpin RNA

Published on: November 1, 2024

1.1K
A Step-By-Step Method to Detect Neutralizing Antibodies Against AAV using a Colorimetric Cell-Based Assay
05:53

A Step-By-Step Method to Detect Neutralizing Antibodies Against AAV using a Colorimetric Cell-Based Assay

Published on: December 7, 2021

4.4K
Author Spotlight: Optimizing Digital Droplet PCR Method for Accurate Adeno-Associated Viral Genome Quantification
04:43

Author Spotlight: Optimizing Digital Droplet PCR Method for Accurate Adeno-Associated Viral Genome Quantification

Published on: October 11, 2024

2.2K

Related Concept Videos

Gene Therapy00:59

Gene Therapy

22.0K
Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be...
22.0K

Articles linked to this work by shared authors, journal, and citation graph.

Future-proofing thalassaemia care: harnessing scalable therapies, artificial intelligence, and global collaboration.

The Lancet. Haematology·2026

Recommendations for harmonizing definition, recording and reporting of the annual bleeding rate (ABR) in hemophilia: Communication from the ISTH SSC Subcommittee on Factor VIII, Factor IX and Rare Coagulation Disorders."

Journal of thrombosis and haemostasis : JTH·2026

Assessment of documentation and reporting methods for annual bleeding rate in hemophilia clinical trials: communication from the ISTH SSC Subcommittee on Factor VIII, Factor IX, and Rare Coagulation Disorders.

Journal of thrombosis and haemostasis : JTH·2026

A Study of Epidermal Elafin Immunohistochemistry as a Diagnostic Biomarker of Acute Skin GVHD.

Indian journal of dermatology·2026

Donor and stem cell source selection in hematopoietic cell transplantation in the Asia-Pacific region: results from the APBMT Activity Survey 2022-2023.

Blood cell therapy·2026

Current Status of National Haemophilia Registries in the Asia-Pacific Region: An AHAD-AP Registry Committee Survey.

Haemophilia : the official journal of the World Federation of Hemophilia·2026

Immunogenicity, safety, and efficacy of rurioctocog alfa pegol in previously untreated patients with severe hemophilia A.

Research and practice in thrombosis and haemostasis·2026

Isolated A1-domain F8 large deletions are associated with favorable immune tolerance induction outcomes in children with severe hemophilia A.

Research and practice in thrombosis and haemostasis·2026

Denecimig (Mim8) prophylaxis in children with hemophilia A with or without factor VIII inhibitors.

Research and practice in thrombosis and haemostasis·2026

Modeling the role of platelet-released polyphosphates in tissue factor-initiated coagulation under flow.

Research and practice in thrombosis and haemostasis·2026

Safety of antithrombotic therapy in hereditary hemorrhagic telangiectasia: results from a prospective cohort study.

Research and practice in thrombosis and haemostasis·2026

Ras-associated autoimmune leukoproliferative disorder associated with immune thrombotic thrombocytopenic purpura.

Research and practice in thrombosis and haemostasis·2026
See all related articles
JoVE
x logofacebook logolinkedin logoyoutube logo
ABOUT JoVE
OverviewLeadershipBlogJoVE Help Center
AUTHORS
Publishing ProcessEditorial BoardScope & PoliciesPeer ReviewFAQSubmit
LIBRARIANS
TestimonialsSubscriptionsAccessResourcesLibrary Advisory BoardFAQ
RESEARCH
JoVE JournalMethods CollectionsJoVE Encyclopedia of ExperimentsArchive
EDUCATION
JoVE CoreJoVE BusinessJoVE Science EducationJoVE Lab ManualFaculty Resource CenterFaculty Site
Terms & Conditions of Use
Privacy Policy
Policies
Jove
Visualize
Contact Us