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Updated: Apr 25, 2026

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In vivo adenine base editing of mutant Galc gene ameliorates Krabbe disease progression

Bae-Geun Nam1,2,3, Jung Hwa Seo1,4, Sung-Ah Hong2

  • 1Department and Research Institute of Rehabilitation Medicine, Yonsei University College of Medicine, Seoul, 03722, Republic of Korea.

Genome Medicine
|April 23, 2026
PubMed
Abstract

No abstract available in PubMed .

Keywords:
GalcKrabbe diseaseadenine base editoradeno-associated virus 9myelination

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