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[Experience with stem cell collection for children with Transfusion-dependent thalassemia undergoing gene therapy]

Meiping Liu1, Yueyue Liang, Wenyan Long

  • 1Department of Pediatrics, 923rd Hospital of the Joint Logistics Support Force of PLA, Nanning, Guangxi 530021, China. 47362636@qq.com.

Zhonghua Yi Xue Yi Chuan Xue Za Zhi = Zhonghua Yixue Yichuanxue Zazhi = Chinese Journal of Medical Genetics
|May 6, 2026
PubMed

Insights

Stem cell collection for gene therapy in transfusion-dependent thalassemia (TDT) children can be challenging. Enhancing mobilization and pre-collection blood transfusions are recommended for successful outcomes.

Area of Science:

  • Pediatric Hematology
  • Gene Therapy
  • Stem Cell Transplantation
Abstract

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