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Updated: May 20, 2026

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Cas13-Mediated RNA Base Editing for the Treatment of Hereditary Hypertrophic Cardiomyopathy

Qun Hu1, Jiajia Lin2, Haodong Cui1,3

  • 1Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, China (Q.H., H.C., X.Z., S.W., M.D., B.W., T.L., X.G., Q.H., Y.L., S.L., H.Y., H.-B.-L., G.L.).

Circulation
|May 18, 2026
PubMed
Abstract

No abstract available in PubMed .

Keywords:
CRISPR-Cas systemsRNA editingcardiomyopathy, hypertrophic

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