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Updated: May 21, 2026

09:50
Digital Droplet PCR Method for the Quantification of AAV Transduction Efficiency in Murine Retina
Published on: December 25, 2021
Pulmonary Alveolar Proteinosis Secondary to ADA-SCID Successfully Treated With Gene Therapy: A Case Report
Cristina de Manuel Gómez1, Patricio Gutiérrez Lucas2, Manuel Parrón-Pajares3
1Paediatric Pulmonology and Cystic Fibrosis Unit, Hospital Universitario La Paz Institute for Health Research-IdiPAZ, Madrid, Spain.
Pediatric Pulmonology
|May 20, 2026
Abstract
No abstract available in PubMed .
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