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Published on: September 13, 2020

Rett syndrome and real-world treatment patterns of trofinetide in the United States

Nazia Rashid1, Vinod Kumar Yakkala2, Safiuddin Shoeb Syed2

  • 1Medical Affairs, Acadia Pharmaceuticals Inc, San Diego, CA, USA.

Journal of Medical Economics
|June 13, 2026
PubMed
Abstract

Keywords:
I10I12I18Rett syndromeadherencereal-world evidencetreatment persistencetrofinetide

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