Related Experiment Video
Updated: Jun 24, 2026

08:35
Production and Titering of Recombinant Adeno-associated Viral Vectors
Published on: November 27, 2011
Promises of co-stimulatory inhibition for durable and repeatable AAV gene therapy
Klaudia Kuranda1, David Alexandre Gross2, Giuseppe Ronzitti2
1Genethon, 91000 Evry, France.
Abstract
No abstract available in PubMed .
Related Concept Videos
Gene Therapy
Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be inserted. The...
Gene Therapy
Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be inserted. The...
