Dual CRISPR/Cas9 correction of compound heterozygous MARS2 mutations in the iPSC line ISMMSi060-A from a patient with

Norman N Liu1, Erdene Baljinnyam2, Ruiqi Hu3

  • 1Division of Genetics and Metabolism, Department of Pediatrics, University of Wisconsin School of Medicine and Public Health, Madison, WI, USA; Center for Precision Medicine, University of Wisconsin School of Medicine and Public Health, Madison, WI, USA.

Stem Cell Research
|June 26, 2026
PubMed

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