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Gene Therapy for Amino Acid Decarboxylase Deficiency: Clinical and Imaging Outcomes in a French Cohort

Clément Dunoyer1, Gaëtan Poulen1, Marie-Céline François-Heude2

  • 1Department of Neurosurgery, Montpellier University Hospital, Montpellier, France.

Movement Disorders : Official Journal of the Movement Disorder Society
|July 2, 2026
PubMed
Abstract

Keywords:
18F‐DOPA PETAromatic L‐amino acid decarboxylase (AADC) deficiencyConvection‐enhanced deliveryEladocagene exuparvovecGene therapyNeuroplasticityPost‐operative dyskinesia

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