Advanced gene editing technologies for oncology mechanisms, applications, and clinical implementation

Soham Bindu1, Archishman Ash1, Koustav Sarkar2

  • 1Department of Biotechnology, School of Bioengineering, SRM Institute of Science and Technology, Chennai, India.

Cancer Gene Therapy
|August 20, 2026
PubMed

Insights

Advanced gene editing technologies like CRISPR offer precise cancer therapies by targeting the hereditary basis of cancer. This review explores their mechanisms, applications, and challenges in clinical oncology.

Area of Science:

  • Oncology and Genetics
  • Molecular Biology and Biotechnology

Background:

  • Gene editing tools revolutionize oncology by enabling targeted therapies for hereditary cancers.
  • Understanding DNA repair mechanisms is crucial for advancing genome editing applications.

Purpose of the Study:

  • To comprehensively review advanced genome editing technologies for cancer treatment.
  • To analyze their mechanisms, applications, challenges, and translational landscape.

Main Methods:

  • Systematic analysis of established (ZFNs, TALENs, CRISPR/Cas) and novel (base editors, prime editors, PASTE) gene editing systems.
  • Examination of hybrid platforms (ARCUS, MegaTALs) integrated with AI and synthetic biology.
  • Review of applications in functional genomics, disease modeling, and direct therapeutic interventions (e.g., CAR-T cell engineering).

Main Results:

  • Detailed examination of gene editing applications across diverse cancer types (lung, breast, colorectal, etc.).
  • Identification of key challenges including delivery, targeting, off-target effects, immunogenicity, and ethical considerations.
  • Analysis of the translational landscape, clinical trials, regulatory aspects, and use of organoid/xenograft models.

Conclusions:

  • Gene editing is transforming cancer medicine, paving the way for more precise and effective personalized therapies.
  • Overcoming delivery and safety challenges is critical for clinical translation.

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