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Lumbar Intrathecal Injection of SOD1-ASOs for Precise CNS Targeting and Predictive Efficacy in Human SOD1-G93A ALS Mice
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Combination Pharmacology for ALS: A Mechanistic Rationale

Jeffrey Rosenfeld1, Shiran Salomon-Zimri2, Ferenc Tracik2

  • 1Center for Restorative Neurology, Department of Neurology, Loma Linda University Health, Loma Linda, CA 92354, USA.

International Journal of Molecular Sciences
|August 27, 2026
PubMed

Keywords:
ALSclinical trialscombination therapymechanistic rationaleneurodegeneration

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