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Updated: Sep 24, 2026

A Standard Methodology to Examine On-site Mutagenicity As a Function of Point Mutation Repair Catalyzed by CRISPR/Cas9 and SsODN in Human Cells
10:07

A Standard Methodology to Examine On-site Mutagenicity As a Function of Point Mutation Repair Catalyzed by CRISPR/Cas9 and SsODN in Human Cells

Published on: August 25, 2017

Therapeutic oligonucleotides as genetic medicines: The current state and future perspective

Bruno Miguel Da Cruz Godinho1, Chantal M Ferguson2, Annemieke Aartsma-Rus3

  • 1Board of Directors, Oligonucleotide Therapeutics Society, San Diego, CA, USA.

Cell Reports. Medicine
|September 22, 2026
PubMed

Keywords:
ASOsRNA interferenceRNA therapeuticsantisensegenetic medicinesiRNAs

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