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Fatal lipid storage disorder

Brain & Development
|January 1, 1984
PubMed

Insights

A 12-week-old infant with acute hepatitis experienced severe lipid accumulation in muscles, mimicking Reye syndrome. This case highlights potential lipid metabolism disorders linked to fulminant hepatic failure.

Area of Science:

  • Pediatric Pathology
  • Hepatology
  • Metabolic Disorders

Background:

  • Reye syndrome is a rare but serious condition that causes swelling in the liver and brain.
  • Acute hepatitis can lead to severe liver dysfunction.

Observation:

  • A 12-week-old infant presented with acute encephalopathy and was diagnosed with acute hepatitis due to positive HBs Ag and liver inflammation.
  • The infant exhibited excessive lipid accumulation in striated muscles, including the biceps brachii, tongue, and cardiac muscles.

Findings:

  • Serum, liver, and muscle carnitine levels were normal.
  • Liver carnitine palmitoyltransferase (CPT) activity was significantly reduced.
  • The findings suggest a potential link between fulminant hepatic failure and abnormal lipid metabolism causing muscle lipidosis.

Implications:

  • This case underscores the importance of considering metabolic investigations in infants with unexplained encephalopathy and liver failure.
  • Understanding the precise metabolic defect could lead to targeted therapies for similar conditions.
  • Further research is needed to elucidate the specific pathway linking hepatic failure to muscle lipid accumulation.

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