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Functional correction of T cells derived from patients with the Wiskott-Aldrich syndrome (WAS) by transduction with an oncoretroviral vector encoding the WAS protein.

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An erythroid-specific chromatin opening element reorganizes beta-globin promoter chromatin structure and augments gene expression.

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Bone marrow-derived cells contribute to tumor neovasculature and, when modified to express an angiogenesis inhibitor, can restrict tumor growth in mice.

Clinical cancer research : an official journal of the American Association for Cancer Research·2001

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Brief report: treatment with azacitidine of patients with end-stage beta-thalassemia

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Slow and Steady Wins The Race? Progress in the Development of Vectors for Gene Therapy of β-Thalassemia and Sickle Cell Disease.

Current status and prospects for gene therapy.

Functional correction of T cells derived from patients with the Wiskott-Aldrich syndrome (WAS) by transduction with an oncoretroviral vector encoding the WAS protein.

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