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Congenital muscular dystrophy with neurological abnormalities: association with Hirschsprung disease

H Mandel1, R Brik, R Ludatscher

  • 1Department of Pediatrics, Rambam Medical Center, Haifa, Israel.

Insights

Congenital muscular dystrophy with neurological issues, known as "CMD Plus," can co-occur with Hirschsprung disease. This suggests a link between muscular dystrophy and visceral nervous system dysfunction.

Area of Science:

  • Neurology
  • Genetics
  • Pediatrics

Background:

  • Congenital muscular dystrophy (CMD) encompasses a group of inherited muscle-weakening disorders.
  • Neurological abnormalities in CMD define the
  • CMD Plus
  • condition, indicating broader systemic involvement.

Observation:

  • A case study of an infant girl with "CMD Plus" also diagnosed with Hirschsprung disease.

Findings:

  • The co-occurrence of "CMD Plus" and Hirschsprung disease suggests a potential link between congenital muscular dystrophy and visceral nervous system abnormalities.
  • This association supports the classification of Hirschsprung disease as an anomaly within the "CMD Plus" spectrum.

Implications:

  • Consider Hirschsprung disease in infants presenting with central nervous system anomalies alongside congenital muscular dystrophy.
  • This finding may lead to a revised understanding of congenital muscular dystrophy, incorporating visceral nervous system involvement.

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