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Engineering Oncogenic Heterozygous Gain-of-Function Mutations in Human Hematopoietic Stem and Progenitor Cells
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Gene therapy, concepts, current trials and future directions

P Tolstoshev1

  • 1Research and Development, Genetic Therapy, Inc., Gaithersburg, Maryland 20878.

Annual Review of Pharmacology and Toxicology
|January 1, 1993
PubMed

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