Gene therapy for cystic fibrosis

A process evaluation of the WHiTE Two trial comparing total hip arthroplasty with and without dual mobility component in the treatment of displaced intracapsular fractures of the proximal femur: Can a trial investigating total hip arthroplasty for hip fracture be delivered in the NHS?

Bone & joint research·2016

Non-viral S/MAR vectors replicate episomally in vivo when provided with a selective advantage.

Gene therapy·2010

Persistent episomal transgene expression in liver following delivery of a scaffold/matrix attachment region containing non-viral vector.

Gene therapy·2008

Lentiviral transduction of the murine lung provides efficient pseudotype and developmental stage-dependent cell-specific transgene expression.

Gene therapy·2008

Intra-amniotic delivery of CFTR-expressing adenovirus does not reverse cystic fibrosis phenotype in inbred CFTR-knockout mice.

Molecular therapy : the journal of the American Society of Gene Therapy·2008

Clinically applicable procedure for gene delivery to fetal gut by ultrasound-guided gastric injection: toward prenatal prevention of early-onset intestinal diseases.

Human gene therapy·2006

Using directed acyclic graphs in observational research: a practical guide for paediatric researchers.

Archives of disease in childhood·2026

Timing and incidence of health conditions recorded during childhood in White British and Pakistani British children: evidence from the Born in Bradford cohort.

Archives of disease in childhood·2026

Trends in neonatal mortality and morbidity at a tertiary centre over four decades: a cohort study.

Archives of disease in childhood·2026

Unplanned discharges and their impact on postdischarge mortality in Ugandan children: a multisite cohort study.

Archives of disease in childhood·2026

Rebuilding child health research capacity in the UK: a national survey of barriers and enablers from the Royal College of Paediatrics and Child Health.

Archives of disease in childhood·2026

International healthcare professionals' competence in caring for LGBTQ+ children and young people: a combined qualitative and quantitative approach.

Archives of disease in childhood·2026

Toward engineered microbial chassis for growth-production balancing.

Synthetic and systems biotechnology·2026

Torsion-spring hypothesis guided pocket-hinge synergistic engineering of glutamate dehydrogenase for efficient synthesis of unnatural amino acids.

Bioresource technology·2026

Carboxymethyl cellulose regulated solvation structures enabling long cyclability in aqueous calcium-ion battery.

International journal of biological macromolecules·2026

Untargeted serum lipidomics reveals lipid metabolic disturbances and identifies candidate lipid biomarkers in acute diquat poisoning.

Toxicology and applied pharmacology·2026

Dual-functional core-shell ZIF-8 with hierarchical pore compartmentalization: Simultaneous ratiometric fluorescence sensing and photocatalytic degradation of oxytetracycline.

Talanta·2026

Covalent immobilization of amyloglucosidase on magnetic-silver nanoparticles for rapid and reusable saccharification of cassava peel.

Carbohydrate research·2026

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Gene therapy for cystic fibrosis

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A process evaluation of the WHiTE Two trial comparing total hip arthroplasty with and without dual mobility component in the treatment of displaced intracapsular fractures of the proximal femur: Can a trial investigating total hip arthroplasty for hip fracture be delivered in the NHS?

Non-viral S/MAR vectors replicate episomally in vivo when provided with a selective advantage.

Persistent episomal transgene expression in liver following delivery of a scaffold/matrix attachment region containing non-viral vector.

Lentiviral transduction of the murine lung provides efficient pseudotype and developmental stage-dependent cell-specific transgene expression.

Intra-amniotic delivery of CFTR-expressing adenovirus does not reverse cystic fibrosis phenotype in inbred CFTR-knockout mice.

Clinically applicable procedure for gene delivery to fetal gut by ultrasound-guided gastric injection: toward prenatal prevention of early-onset intestinal diseases.

Using directed acyclic graphs in observational research: a practical guide for paediatric researchers.

Timing and incidence of health conditions recorded during childhood in White British and Pakistani British children: evidence from the Born in Bradford cohort.

Trends in neonatal mortality and morbidity at a tertiary centre over four decades: a cohort study.

Unplanned discharges and their impact on postdischarge mortality in Ugandan children: a multisite cohort study.

Rebuilding child health research capacity in the UK: a national survey of barriers and enablers from the Royal College of Paediatrics and Child Health.

International healthcare professionals' competence in caring for LGBTQ+ children and young people: a combined qualitative and quantitative approach.

Toward engineered microbial chassis for growth-production balancing.

Torsion-spring hypothesis guided pocket-hinge synergistic engineering of glutamate dehydrogenase for efficient synthesis of unnatural amino acids.

Carboxymethyl cellulose regulated solvation structures enabling long cyclability in aqueous calcium-ion battery.

Untargeted serum lipidomics reveals lipid metabolic disturbances and identifies candidate lipid biomarkers in acute diquat poisoning.

Dual-functional core-shell ZIF-8 with hierarchical pore compartmentalization: Simultaneous ratiometric fluorescence sensing and photocatalytic degradation of oxytetracycline.

Covalent immobilization of amyloglucosidase on magnetic-silver nanoparticles for rapid and reusable saccharification of cassava peel.

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Gene therapy for cystic fibrosis

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