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Retinal dystrophy in long chain 3-hydroxy-acyl-coA dehydrogenase deficiency

I Schrijver-Wieling1, G H van Rens, D Wittebol-Post

  • 1Department of Ophthalmology, University Hospital Utrecht, The Netherlands.

Summary

Long chain 3-hydroxyacyl-CoA-dehydrogenase (LCHAD) deficiency, crucial for fatty acid breakdown, can cause severe hypoglycemia. Early diagnosis and dietary management are vital for improving life expectancy and preventing vision loss in affected children.

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