Bone marrow transplantation for the treatment of alpha-mannosidosis

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Bone marrow transplantation for the treatment of alpha-mannosidosis

Related Concept Videos

Prospective characterization of early symptom onset and progression in young pediatric patients with variants in the G LA gene across 5 years: Longitudinal data from the Fabry MOPPet Study.

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Bone marrow transplantation for the treatment of alpha-mannosidosis

Abstract:

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