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Biology Direct
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September 13, 2023
Preliminary insights into RNA in CSF of pediatric SMA patients after 6 months of nusinersen
M Garofalo, S Bonanno, S Marcuzzo, et al.
Journal of Neurology
|
June 24, 2025
Quantitative cervical cord MRI in spinal muscular atrophy: a sensitive imaging biomarker of disease evolution and treatment
C Asteggiano, L Mazzocchi, L Farina, et al.
Journal of the Neurological Sciences
|
October 13, 2010
New molecular findings in congenital myopathies due to selenoprotein N gene mutations
R Cagliani, M E Fruguglietti, A Berardinelli, et al.
Neuromuscular Disorders : NMD
|
April 17, 2007
The Hammersmith functional score correlates with the SMN2 copy number: a multicentric study
F D Tiziano, E Bertini, S Messina, et al.
Neuromuscular Disorders : NMD
|
June 26, 2012
Respiratory and cardiac function in congenital muscular dystrophies with alpha dystroglycan deficiency
M Pane, S Messina, G Vasco, et al.
Neurology
|
November 4, 2006
Randomized, double-blind, placebo-controlled trial of phenylbutyrate in spinal muscular atrophy
E Mercuri, E Bertini, S Messina, et al.
Neuromuscular Disorders : NMD
|
January 24, 2006
Reliability of the Hammersmith functional motor scale for spinal muscular atrophy in a multicentric study
E Mercuri, S Messina, R Battini, et al.
Neurology
|
March 23, 2007
Phenotypic clustering of lamin A/C mutations in neuromuscular patients
S Benedetti, I Menditto, M Degano, et al.
Neurology
|
September 8, 2010
Congenital muscular dystrophies with cognitive impairment. A population study
S Messina, C Bruno, I Moroni, et al.
Neuromuscular Disorders : NMD
|
June 3, 2008
POMT1 and POMT2 mutations in CMD patients: a multicentric Italian study
S Messina, M Mora, E Pegoraro, et al.
Page
of 4
Search research articles
Search
Showing results (21-30 of 34) with videos related to
Sort By:
Page
of 4
Biology Direct
|
September 13, 2023
Preliminary insights into RNA in CSF of pediatric SMA patients after 6 months of nusinersen
M Garofalo, S Bonanno, S Marcuzzo, et al.
Journal of Neurology
|
June 24, 2025
Quantitative cervical cord MRI in spinal muscular atrophy: a sensitive imaging biomarker of disease evolution and treatment
C Asteggiano, L Mazzocchi, L Farina, et al.
Journal of the Neurological Sciences
|
October 13, 2010
New molecular findings in congenital myopathies due to selenoprotein N gene mutations
R Cagliani, M E Fruguglietti, A Berardinelli, et al.
Neuromuscular Disorders : NMD
|
April 17, 2007
The Hammersmith functional score correlates with the SMN2 copy number: a multicentric study
F D Tiziano, E Bertini, S Messina, et al.
Neuromuscular Disorders : NMD
|
June 26, 2012
Respiratory and cardiac function in congenital muscular dystrophies with alpha dystroglycan deficiency
M Pane, S Messina, G Vasco, et al.
Neurology
|
November 4, 2006
Randomized, double-blind, placebo-controlled trial of phenylbutyrate in spinal muscular atrophy
E Mercuri, E Bertini, S Messina, et al.
Neuromuscular Disorders : NMD
|
January 24, 2006
Reliability of the Hammersmith functional motor scale for spinal muscular atrophy in a multicentric study
E Mercuri, S Messina, R Battini, et al.
Neurology
|
March 23, 2007
Phenotypic clustering of lamin A/C mutations in neuromuscular patients
S Benedetti, I Menditto, M Degano, et al.
Neurology
|
September 8, 2010
Congenital muscular dystrophies with cognitive impairment. A population study
S Messina, C Bruno, I Moroni, et al.
Neuromuscular Disorders : NMD
|
June 3, 2008
POMT1 and POMT2 mutations in CMD patients: a multicentric Italian study
S Messina, M Mora, E Pegoraro, et al.
Page
of 4