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Neuromuscular Disorders : NMD
|
August 22, 2020
Cardiac MRI identifies valvular and myocardial disease in a subset of ANO5-related muscular dystrophy patients
Ranjini Srinivasan, Pomi Yun, Sarah Neuhaus, et al.
Archives of Physical Medicine and Rehabilitation
|
November 9, 2020
Responsiveness and Minimal Clinically Important Difference of the Motor Function Measure in Collagen VI-Related Dystrophies and Laminin Alpha2-Related Muscular Dystrophy
Laure Le Goff, Katherine G Meilleur, Gina Norato, et al.
BMC Pediatrics
|
February 8, 2020
Hypoglycemia in patients with congenital muscle disease
Leslie H Hayes, Pomi Yun, Payam Mohassel, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 8, 2021
Ethical challenges for a new generation of early-phase pediatric gene therapy trials
Alexander A Iyer, Dimah Saade, Diana Bharucha-Goebel, et al.
HGG Advances
|
September 25, 2024
Differential inclusion of NEB exons 143 and 144 provides insight into NEB-related myopathy variant interpretation and disease manifestation
Sarah Silverstein, Rotem Orbach, Safoora Syeda, et al.
Journal of Neuromuscular Diseases
|
June 16, 2020
Lower Extremity Muscle Involvement in the Intermediate and Bethlem Myopathy Forms of COL6-Related Dystrophy and Duchenne Muscular Dystrophy: A Cross-Sectional Study
Abhinandan Batra, Donovan J Lott, Rebecca Willcocks, et al.
Medrxiv : the Preprint Server for Health Sciences
|
April 8, 2024
Differential inclusion of <i>NEB</i> exons 143 and 144 provides insight into <i>NEB</i>-related myopathy variant interpretation and disease manifestation
Sarah Silverstein, Rotem Orbach, Safoora Syeda, et al.
Annals of Clinical and Translational Neurology
|
November 3, 2021
Transcriptome analysis of collagen VI-related muscular dystrophy muscle biopsies
Eleonora Guadagnin, Payam Mohassel, Kory R Johnson, et al.
Journal of Neuromuscular Diseases
|
September 10, 2019
Identification of a Novel Deep Intronic Mutation in CAPN3 Presenting a Promising Target for Therapeutic Splice Modulation
Ying Hu, Payam Mohassel, Sandra Donkervoort, et al.
Clinical Therapeutics
|
April 26, 2024
Lessons Learned From Clinical Studies in Centronuclear Myopathies: The Patient Perspective-A Qualitative Study
Lizan Stinissen, Johann Böhm, Sietse Bouma, et al.
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Search research articles
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Showing results (21-30 of 114) with videos related to
Sort By:
Page
of 12
Neuromuscular Disorders : NMD
|
August 22, 2020
Cardiac MRI identifies valvular and myocardial disease in a subset of ANO5-related muscular dystrophy patients
Ranjini Srinivasan, Pomi Yun, Sarah Neuhaus, et al.
Archives of Physical Medicine and Rehabilitation
|
November 9, 2020
Responsiveness and Minimal Clinically Important Difference of the Motor Function Measure in Collagen VI-Related Dystrophies and Laminin Alpha2-Related Muscular Dystrophy
Laure Le Goff, Katherine G Meilleur, Gina Norato, et al.
BMC Pediatrics
|
February 8, 2020
Hypoglycemia in patients with congenital muscle disease
Leslie H Hayes, Pomi Yun, Payam Mohassel, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 8, 2021
Ethical challenges for a new generation of early-phase pediatric gene therapy trials
Alexander A Iyer, Dimah Saade, Diana Bharucha-Goebel, et al.
HGG Advances
|
September 25, 2024
Differential inclusion of NEB exons 143 and 144 provides insight into NEB-related myopathy variant interpretation and disease manifestation
Sarah Silverstein, Rotem Orbach, Safoora Syeda, et al.
Journal of Neuromuscular Diseases
|
June 16, 2020
Lower Extremity Muscle Involvement in the Intermediate and Bethlem Myopathy Forms of COL6-Related Dystrophy and Duchenne Muscular Dystrophy: A Cross-Sectional Study
Abhinandan Batra, Donovan J Lott, Rebecca Willcocks, et al.
Medrxiv : the Preprint Server for Health Sciences
|
April 8, 2024
Differential inclusion of <i>NEB</i> exons 143 and 144 provides insight into <i>NEB</i>-related myopathy variant interpretation and disease manifestation
Sarah Silverstein, Rotem Orbach, Safoora Syeda, et al.
Annals of Clinical and Translational Neurology
|
November 3, 2021
Transcriptome analysis of collagen VI-related muscular dystrophy muscle biopsies
Eleonora Guadagnin, Payam Mohassel, Kory R Johnson, et al.
Journal of Neuromuscular Diseases
|
September 10, 2019
Identification of a Novel Deep Intronic Mutation in CAPN3 Presenting a Promising Target for Therapeutic Splice Modulation
Ying Hu, Payam Mohassel, Sandra Donkervoort, et al.
Clinical Therapeutics
|
April 26, 2024
Lessons Learned From Clinical Studies in Centronuclear Myopathies: The Patient Perspective-A Qualitative Study
Lizan Stinissen, Johann Böhm, Sietse Bouma, et al.
Page
of 12