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Molecular Genetics and Metabolism
|
June 29, 2021
Childhood-onset hereditary spastic paraplegia and its treatable mimics
Darius Ebrahimi-Fakhari, Afshin Saffari, Phillip L Pearl
Autophagy
|
January 26, 2017
Using tuberous sclerosis complex to understand the impact of MTORC1 signaling on mitochondrial dynamics and mitophagy in neurons
Darius Ebrahimi-Fakhari, Afshin Saffari, Lara Wahlster, et al.
Orphanet Journal of Rare Diseases
|
January 6, 2025
Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol
Jan H Driedger, Julian Schröter, , et al.
Der Nervenarzt
|
July 10, 2019
[Gene therapies for neuromuscular diseases]
Afshin Saffari, Markus Weiler, Georg Friedrich Hoffmann, et al.
Brain : a Journal of Neurology
|
November 25, 2015
The evolving spectrum of PRRT2-associated paroxysmal diseases
Darius Ebrahimi-Fakhari, Afshin Saffari, Ana Westenberger, et al.
Annals of Clinical and Translational Neurology
|
January 19, 2019
Novel challenges in spinal muscular atrophy - How to screen and whom to treat?
Afshin Saffari, Stefan Kölker, Georg F Hoffmann, et al.
Human Molecular Genetics
|
August 4, 2022
De novo variants cause complex symptoms in HSP-ATL1 (SPG3A) and uncover genotype-phenotype correlations
Julian E Alecu, Afshin Saffari, Catherine Jordan, et al.
Neuropediatrics
|
February 12, 2020
Axenfeld-Rieger Anomaly and Neuropsychiatric Problems-More than Meets the Eye
Afshin Saffari, Andreas Ziegler, Andreas Merkenschlager, et al.
American Journal of Medical Genetics. Part A
|
August 17, 2022
Upper motor neuron signs and early onset gait abnormalities in young children with bi-allelic VWA1 variants
Dustin L Gable, Alisa Mo, Elicia Estrella, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 28, 2024
Quantitative natural history modeling of HPDL-related disease based on cross-sectional data reveals genotype-phenotype correlations
Julian E Alecu, Amy Tam, Silja Richter, et al.
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of 5
Search research articles
Search
Showing results (1-10 of 46) with videos related to
Sort By:
Page
of 5
Molecular Genetics and Metabolism
|
June 29, 2021
Childhood-onset hereditary spastic paraplegia and its treatable mimics
Darius Ebrahimi-Fakhari, Afshin Saffari, Phillip L Pearl
Autophagy
|
January 26, 2017
Using tuberous sclerosis complex to understand the impact of MTORC1 signaling on mitochondrial dynamics and mitophagy in neurons
Darius Ebrahimi-Fakhari, Afshin Saffari, Lara Wahlster, et al.
Orphanet Journal of Rare Diseases
|
January 6, 2025
Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol
Jan H Driedger, Julian Schröter, , et al.
Der Nervenarzt
|
July 10, 2019
[Gene therapies for neuromuscular diseases]
Afshin Saffari, Markus Weiler, Georg Friedrich Hoffmann, et al.
Brain : a Journal of Neurology
|
November 25, 2015
The evolving spectrum of PRRT2-associated paroxysmal diseases
Darius Ebrahimi-Fakhari, Afshin Saffari, Ana Westenberger, et al.
Annals of Clinical and Translational Neurology
|
January 19, 2019
Novel challenges in spinal muscular atrophy - How to screen and whom to treat?
Afshin Saffari, Stefan Kölker, Georg F Hoffmann, et al.
Human Molecular Genetics
|
August 4, 2022
De novo variants cause complex symptoms in HSP-ATL1 (SPG3A) and uncover genotype-phenotype correlations
Julian E Alecu, Afshin Saffari, Catherine Jordan, et al.
Neuropediatrics
|
February 12, 2020
Axenfeld-Rieger Anomaly and Neuropsychiatric Problems-More than Meets the Eye
Afshin Saffari, Andreas Ziegler, Andreas Merkenschlager, et al.
American Journal of Medical Genetics. Part A
|
August 17, 2022
Upper motor neuron signs and early onset gait abnormalities in young children with bi-allelic VWA1 variants
Dustin L Gable, Alisa Mo, Elicia Estrella, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 28, 2024
Quantitative natural history modeling of HPDL-related disease based on cross-sectional data reveals genotype-phenotype correlations
Julian E Alecu, Amy Tam, Silja Richter, et al.
Page
of 5