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Human Molecular Genetics
|
April 24, 2016
In vitro and in vivo rescue of aberrant splicing in CEP290-associated LCA by antisense oligonucleotide delivery
Alejandro Garanto, Daniel C Chung, Lonneke Duijkers, et al.
Stem Cell Research
|
May 8, 2022
Generation of an iPSC line (SCTCi015-A) and isogenic control line (SCTCi015-A-1) from an age-related macular degeneration patient carrying the variant c.355G>A in the CFI gene
Sarah de Jong, Louet Koolen, Irene Vázquez-Domínguez, et al.
International Journal of Molecular Sciences
|
March 10, 2018
Antisense Oligonucleotide-Based Splicing Correction in Individuals with Leber Congenital Amaurosis due to Compound Heterozygosity for the c.2991+1655A>G Mutation in CEP290
Lonneke Duijkers, L Ingeborgh van den Born, John Neidhardt, et al.
Plos One
|
March 3, 2016
Expression Atlas of the Deubiquitinating Enzymes in the Adult Mouse Retina, Their Evolutionary Diversification and Phenotypic Roles
Mariona Esquerdo, Xavier Grau-Bové, Alejandro Garanto, et al.
Stem Cell Research
|
February 5, 2022
Generation of a patient-derived induced pluripotent cell line (SCTCi016-A) carrying a homozygous variant in RPE65
Irene Vázquez-Domínguez, Michael Kwint, Hester Y Kroes, et al.
Journal of Inherited Metabolic Disease
|
April 6, 2023
Exploring genotype-phenotype correlations in glutaric aciduria type 1
Imke M E Schuurmans, Bianca Dimitrov, Julian Schröter, et al.
Glycobiology
|
May 18, 2026
Cellular homeostasis of N-acetylneuraminic acid and non-canonical sialic acids is mediated by human N-acetylneuraminate lyase
Sjanie Huang, Iris Harmsen, Moritz Rahm, et al.
Investigative Ophthalmology & Visual Science
|
February 26, 2020
Modeling ZNF408-Associated FEVR in Zebrafish Results in Abnormal Retinal Vasculature
Dyah W Karjosukarso, Zaheer Ali, Theo A Peters, et al.
Progress in Retinal and Eye Research
|
February 21, 2021
Implications of genetic variation in the complement system in age-related macular degeneration
Sarah de Jong, Giuliana Gagliardi, Alejandro Garanto, et al.
American Journal of Human Genetics
|
March 13, 2018
Identification and Rescue of Splice Defects Caused by Two Neighboring Deep-Intronic ABCA4 Mutations Underlying Stargardt Disease
Silvia Albert, Alejandro Garanto, Riccardo Sangermano, et al.
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of 9
Search research articles
Search
Showing results (41-50 of 82) with videos related to
Sort By:
Page
of 9
Human Molecular Genetics
|
April 24, 2016
In vitro and in vivo rescue of aberrant splicing in CEP290-associated LCA by antisense oligonucleotide delivery
Alejandro Garanto, Daniel C Chung, Lonneke Duijkers, et al.
Stem Cell Research
|
May 8, 2022
Generation of an iPSC line (SCTCi015-A) and isogenic control line (SCTCi015-A-1) from an age-related macular degeneration patient carrying the variant c.355G>A in the CFI gene
Sarah de Jong, Louet Koolen, Irene Vázquez-Domínguez, et al.
International Journal of Molecular Sciences
|
March 10, 2018
Antisense Oligonucleotide-Based Splicing Correction in Individuals with Leber Congenital Amaurosis due to Compound Heterozygosity for the c.2991+1655A>G Mutation in CEP290
Lonneke Duijkers, L Ingeborgh van den Born, John Neidhardt, et al.
Plos One
|
March 3, 2016
Expression Atlas of the Deubiquitinating Enzymes in the Adult Mouse Retina, Their Evolutionary Diversification and Phenotypic Roles
Mariona Esquerdo, Xavier Grau-Bové, Alejandro Garanto, et al.
Stem Cell Research
|
February 5, 2022
Generation of a patient-derived induced pluripotent cell line (SCTCi016-A) carrying a homozygous variant in RPE65
Irene Vázquez-Domínguez, Michael Kwint, Hester Y Kroes, et al.
Journal of Inherited Metabolic Disease
|
April 6, 2023
Exploring genotype-phenotype correlations in glutaric aciduria type 1
Imke M E Schuurmans, Bianca Dimitrov, Julian Schröter, et al.
Glycobiology
|
May 18, 2026
Cellular homeostasis of N-acetylneuraminic acid and non-canonical sialic acids is mediated by human N-acetylneuraminate lyase
Sjanie Huang, Iris Harmsen, Moritz Rahm, et al.
Investigative Ophthalmology & Visual Science
|
February 26, 2020
Modeling ZNF408-Associated FEVR in Zebrafish Results in Abnormal Retinal Vasculature
Dyah W Karjosukarso, Zaheer Ali, Theo A Peters, et al.
Progress in Retinal and Eye Research
|
February 21, 2021
Implications of genetic variation in the complement system in age-related macular degeneration
Sarah de Jong, Giuliana Gagliardi, Alejandro Garanto, et al.
American Journal of Human Genetics
|
March 13, 2018
Identification and Rescue of Splice Defects Caused by Two Neighboring Deep-Intronic ABCA4 Mutations Underlying Stargardt Disease
Silvia Albert, Alejandro Garanto, Riccardo Sangermano, et al.
Page
of 9