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Human Gene Therapy
|
December 7, 2011
Gene therapy for retinitis pigmentosa caused by MFRP mutations: human phenotype and preliminary proof of concept
Astra Dinculescu, Jackie Estreicher, Juan C Zenteno, et al.
Archives of Ophthalmology (Chicago, Ill. : 1960)
|
September 14, 2011
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years
Samuel G Jacobson, Artur V Cideciyan, Ramakrishna Ratnakaram, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 2, 2025
Recovery of cone-mediated vision in Lebercilin associated retinal ciliopathy after gene therapy: One-year results of a phase I/II trial
Tomas S Aleman, Katherine E Uyhazi, Alejandro J Roman, et al.
Investigative Ophthalmology & Visual Science
|
December 18, 2024
Retinal Degeneration Associated With Biallelic RDH12 Variants: Longitudinal Evaluation of Retinal Structure and Visual Function in Pediatric Patients
Tomas S Aleman, Alejandro J Roman, Katherine E Uyhazi, et al.
Nature Medicine
|
December 19, 2018
Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, et al.
Nature Medicine
|
April 5, 2022
Intravitreal antisense oligonucleotide sepofarsen in Leber congenital amaurosis type 10: a phase 1b/2 trial
Stephen R Russell, Arlene V Drack, Artur V Cideciyan, et al.
Page
of 10
Search research articles
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Showing results (91-100 of 96) with videos related to
Sort By:
Page
of 10
You have reached the last page of results.
This site can display upto 96 results.
Human Gene Therapy
|
December 7, 2011
Gene therapy for retinitis pigmentosa caused by MFRP mutations: human phenotype and preliminary proof of concept
Astra Dinculescu, Jackie Estreicher, Juan C Zenteno, et al.
Archives of Ophthalmology (Chicago, Ill. : 1960)
|
September 14, 2011
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years
Samuel G Jacobson, Artur V Cideciyan, Ramakrishna Ratnakaram, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 2, 2025
Recovery of cone-mediated vision in Lebercilin associated retinal ciliopathy after gene therapy: One-year results of a phase I/II trial
Tomas S Aleman, Katherine E Uyhazi, Alejandro J Roman, et al.
Investigative Ophthalmology & Visual Science
|
December 18, 2024
Retinal Degeneration Associated With Biallelic RDH12 Variants: Longitudinal Evaluation of Retinal Structure and Visual Function in Pediatric Patients
Tomas S Aleman, Alejandro J Roman, Katherine E Uyhazi, et al.
Nature Medicine
|
December 19, 2018
Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, et al.
Nature Medicine
|
April 5, 2022
Intravitreal antisense oligonucleotide sepofarsen in Leber congenital amaurosis type 10: a phase 1b/2 trial
Stephen R Russell, Arlene V Drack, Artur V Cideciyan, et al.
Page
of 10