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Molecular Therapy : the Journal of the American Society of Gene Therapy|April 9, 2017
Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New IndicationsAlessandra BiffiCurrent Gene Therapy|September 1, 2012
Genetically-modified hematopoietic stem cells and their progeny for widespread and efficient protein delivery to diseased sites: the case of lysosomal storage disordersAlessandra BiffiHuman Molecular Genetics|November 26, 2015
Gene therapy for lysosomal storage disorders: a good startAlessandra BiffiHematology/Oncology Clinics of North America|September 13, 2017
Hematopoietic Gene Therapies for Metabolic and Neurologic DiseasesAlessandra BiffiNeurotherapeutics : the Journal of the American Society for Experimental Neurotherapeutics|September 14, 2024
Hematopoietic stem cell gene therapy to halt neurodegenerationAlessandra BiffiCell Stem Cell|April 7, 2015
Clinical translation of TALENS: Treating SCID-X1 by gene editing in iPSCsAlessandra BiffiCurrent Opinion in Hematology|May 4, 2011
Maintenance of a functional hematopoietic stem cell niche through galactocerebrosidase and other enzymesIlaria Visigalli, Alessandra BiffiHuman Gene Therapy|August 10, 2019
Gene-Based Approaches to Inherited Neurometabolic DiseasesValentina Poletti, Alessandra BiffiExpert Opinion on Biological Therapy|August 21, 2007
Novel candidate disease for gene therapy: metachromatic leukodystrophyAlessandra Biffi, Luigi NaldiniCurrent Gene Therapy|April 9, 2008
Human hematopoietic stem cells in gene therapy: pre-clinical and clinical issuesAlessandra Biffi, Martina CesaniPageof 16