Showing results (1-10 of 187) with videos related to
Sort By:
Pageof 19
Methods in Molecular Biology (Clifton, N.J.)|March 29, 2012
Exon skipping quantification by real-time PCRAlessandra Ferlini, Paola RimessiJournal of Neuromuscular Diseases|August 7, 2023
Biomarkers in Duchenne Muscular Dystrophy: Current Status and Future DirectionsFernanda Fortunato, Alessandra FerliniJournal of Clinical Medicine|May 11, 2019
Urinary Stem Cells as Tools to Study Genetic Disease: Overview of the LiteratureMaria Sofia Falzarano, Alessandra FerliniNeuromuscular Disorders : NMD|November 3, 2012
The medical genetics of dystrophinopathies: molecular genetic diagnosis and its impact on clinical practiceAlessandra Ferlini, Marcella Neri, Francesca GualandiNeuromuscular Disorders : NMD|November 5, 2021
The DMD gene and therapeutic approaches to restore dystrophinFernanda Fortunato, Marianna Farnè, Alessandra FerliniInternational Journal of Molecular Sciences|October 3, 2013
Non-coding RNAs in muscle dystrophiesDaniela Erriquez, Giovanni Perini, Alessandra FerliniThe Lancet. Neurology|November 26, 2003
Dystrophin and mutations: one gene, several proteins, multiple phenotypesFrancesco Muntoni, Silvia Torelli, Alessandra FerliniOrphanet Journal of Rare Diseases|October 4, 2023
Rare diseases' genetic newborn screening as the gateway to future genomic medicine: the Screen4Care EU-IMI projectAlessandra Ferlini, Edith Sky Gross, Nicolas Garnier, et al.Nucleic Acid Therapeutics|February 11, 2014
Nanoparticle delivery of antisense oligonucleotides and their application in the exon skipping strategy for Duchenne muscular dystrophyMaria Sofia Falzarano, Chiara Passarelli, Alessandra FerliniNpj Imaging|March 24, 2026
Correlative multimodal imaging for microscale spatial mapping of collagen-gene activity interactions in human tissuesRiccardo Scodellaro, Martina Mietto, Alessandra Ferlini, et al.Pageof 19