Showing results (101-110 of 131) with videos related to
Sort By:
Pageof 14
Molecular Therapy. Methods & Clinical Development|August 25, 2018
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease PhenotypeLeslie Weber, Valentina Poletti, Elisa Magrin, et al.Stem Cell Reports|February 11, 2014
Long-term stability and safety of transgenic cultured epidermal stem cells in gene therapy of junctional epidermolysis bullosaLaura De Rosa, Sonia Carulli, Fabienne Cocchiarella, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|August 21, 2018
CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa PatientDaniela Benati, Francesca Miselli, Fabienne Cocchiarella, et al.American Journal of Physiology. Heart and Circulatory Physiology|April 30, 2026
The Medium Chain Fatty Acid Octanoate is a Beneficial Fuel for the Failing HeartNikoloz Gorgodze, Timothy R Matsuura, Noemi Nisini, et al.EMBO Molecular Medicine|July 29, 2010
Correction of beta-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patientsEmanuela Anna Roselli, Riccardo Mezzadra, Marta Claudia Frittoli, et al.Scientific Reports|April 21, 2016
Transcriptional, epigenetic and retroviral signatures identify regulatory regions involved in hematopoietic lineage commitmentOriana Romano, Clelia Peano, Guidantonio Malagoli Tagliazucchi, et al.Frontiers in Veterinary Science|February 11, 2026
Signalment, clinical characteristics, and echocardiographic findings in dogs affected by secondary atrial fibrillation with and without concomitant frequent and complex ventricular arrhythmiasGiovanni Romito, Chiara Mazzoldi, Chiara Riccio, et al.Molecular Therapy. Methods & Clinical Development|October 16, 2018
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-ThalassemiaMaria Rosa Lidonnici, Ylenia Paleari, Francesca Tiboni, et al.Journal of Experimental & Clinical Cancer Research : CR|November 16, 2021
Alternative splicing of NF-YA promotes prostate cancer aggressiveness and represents a new molecular marker for clinical stratification of patientsSilvia Belluti, Valentina Semeghini, Giovanna Rigillo, et al.Biomolecules|November 27, 2024
Restored Collagen VI Microfilaments Network in the Extracellular Matrix of CRISPR-Edited Ullrich Congenital Muscular Dystrophy FibroblastsDaniela Benati, Eleonora Cattin, Federico Corradi, et al.Pageof 14