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The EMBO Journal
|
June 18, 2004
Binding of the 7SK snRNA turns the HEXIM1 protein into a P-TEFb (CDK9/cyclin T) inhibitor
Annemieke A Michels, Alessandro Fraldi, Qintong Li, et al.
Annals of the Rheumatic Diseases
|
November 3, 2012
Autophagy contributes to inflammation in patients with TNFR-associated periodic syndrome (TRAPS)
Tiziana Bachetti, Sabrina Chiesa, Patrizio Castagnola, et al.
Developmental Cell
|
September 6, 2011
Transcriptional activation of lysosomal exocytosis promotes cellular clearance
Diego L Medina, Alessandro Fraldi, Valentina Bouche, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 19, 2022
The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease
Antonio Monaco, Veronica Maffia, Nicolina Cristina Sorrentino, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
February 23, 2020
The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease
Antonio Monaco, Veronica Maffia, Nicolina Cristina Sorrentino, et al.
Molecular Therapy. Methods & Clinical Development
|
December 3, 2019
Enhancing the Therapeutic Potential of Sulfamidase for the Treatment of Mucopolysaccharidosis IIIA
Nicolina Cristina Sorrentino, Vincenzo Cacace, Maria De Risi, et al.
Human Gene Therapy
|
February 15, 2014
Intracerebral administration of adeno-associated viral vector serotype rh.10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type IIIA disease: results of a phase I/II trial
Marc Tardieu, Michel Zérah, Béatrice Husson, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 8, 2015
A Comprehensive Map of CNS Transduction by Eight Recombinant Adeno-associated Virus Serotypes Upon Cerebrospinal Fluid Administration in Pigs
Nicolina Cristina Sorrentino, Veronica Maffia, Sandra Strollo, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
September 29, 2024
Anti-amyloid treatment is broadly effective in neuronopathic mucopolysaccharidoses and synergizes with gene therapy in MPS-IIIA
Marianna Giaccio, Antonio Monaco, Laura Galiano, et al.
Nature Communications
|
June 10, 2021
Altered heparan sulfate metabolism during development triggers dopamine-dependent autistic-behaviours in models of lysosomal storage disorders
Maria De Risi, Michele Tufano, Filomena Grazia Alvino, et al.
Page
of 5
Search research articles
Search
Showing results (31-40 of 42) with videos related to
Sort By:
Page
of 5
The EMBO Journal
|
June 18, 2004
Binding of the 7SK snRNA turns the HEXIM1 protein into a P-TEFb (CDK9/cyclin T) inhibitor
Annemieke A Michels, Alessandro Fraldi, Qintong Li, et al.
Annals of the Rheumatic Diseases
|
November 3, 2012
Autophagy contributes to inflammation in patients with TNFR-associated periodic syndrome (TRAPS)
Tiziana Bachetti, Sabrina Chiesa, Patrizio Castagnola, et al.
Developmental Cell
|
September 6, 2011
Transcriptional activation of lysosomal exocytosis promotes cellular clearance
Diego L Medina, Alessandro Fraldi, Valentina Bouche, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 19, 2022
The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease
Antonio Monaco, Veronica Maffia, Nicolina Cristina Sorrentino, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
February 23, 2020
The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease
Antonio Monaco, Veronica Maffia, Nicolina Cristina Sorrentino, et al.
Molecular Therapy. Methods & Clinical Development
|
December 3, 2019
Enhancing the Therapeutic Potential of Sulfamidase for the Treatment of Mucopolysaccharidosis IIIA
Nicolina Cristina Sorrentino, Vincenzo Cacace, Maria De Risi, et al.
Human Gene Therapy
|
February 15, 2014
Intracerebral administration of adeno-associated viral vector serotype rh.10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type IIIA disease: results of a phase I/II trial
Marc Tardieu, Michel Zérah, Béatrice Husson, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 8, 2015
A Comprehensive Map of CNS Transduction by Eight Recombinant Adeno-associated Virus Serotypes Upon Cerebrospinal Fluid Administration in Pigs
Nicolina Cristina Sorrentino, Veronica Maffia, Sandra Strollo, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
September 29, 2024
Anti-amyloid treatment is broadly effective in neuronopathic mucopolysaccharidoses and synergizes with gene therapy in MPS-IIIA
Marianna Giaccio, Antonio Monaco, Laura Galiano, et al.
Nature Communications
|
June 10, 2021
Altered heparan sulfate metabolism during development triggers dopamine-dependent autistic-behaviours in models of lysosomal storage disorders
Maria De Risi, Michele Tufano, Filomena Grazia Alvino, et al.
Page
of 5