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International Journal of Molecular Sciences|August 28, 2025
Prime Editing Modification with FEN1 Improves F508del Variant Editing in the <i>CFTR</i> Gene in Airway Basal CellsOlga V Volodina, Anna G Demchenko, Arina A Anuchina, et al.Plos One|November 11, 2020
P.F508del editing in cells from cystic fibrosis patientsSvetlana A Smirnikhina, Ekaterina V Kondrateva, Elmira P Adilgereeva, et al.Genetics in Medicine : Official Journal of the American College of Medical Genetics|April 7, 2021
Biallelic variants in TMEM222 cause a new autosomal recessive neurodevelopmental disorderDaniel L Polla, Mohammad Ali Farazi Fard, Zahra Tabatabaei, et al.Pageof 3