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Molecular Genetics and Metabolism
|
December 7, 2024
Clinical and biochemical abnormalities in a feline model of GM2 activator deficiency
Sidney J Beecy, Amanda L Gross, Anne S Maguire, et al.
Biorxiv : the Preprint Server for Biology
|
November 28, 2024
Intravenous gene therapy improves lifespan and clinical outcomes in feline Sandhoff Disease
Anne S Maguire, Linh Ta, Amanda L Gross, et al.
Molecular Therapy. Methods & Clinical Development
|
November 2, 2022
AAVrh10 vector corrects pathology in animal models of GM1 gangliosidosis and achieves widespread distribution in the CNS of nonhuman primates
Michaël Hocquemiller, Laura Giersch, Xin Mei, et al.
The International Journal of Neuropsychopharmacology
|
December 14, 2018
Positive N-Methyl-D-Aspartate Receptor Modulation by Rapastinel Promotes Rapid and Sustained Antidepressant-Like Effects
John E Donello, Pradeep Banerjee, Yong-Xin Li, et al.
Brain : a Journal of Neurology
|
August 19, 2021
Intravenous delivery of adeno-associated viral gene therapy in feline GM1 gangliosidosis
Amanda L Gross, Heather L Gray-Edwards, Cassie N Bebout, et al.
Ebiomedicine
|
June 2, 2023
A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosis
Pamela Kell, Rohini Sidhu, Mingxing Qian, et al.
Neuroscience
|
November 7, 2016
AAV-mediated gene delivery attenuates neuroinflammation in feline Sandhoff disease
Allison M Bradbury, Tiffany A Peterson, Amanda L Gross, et al.
Molecular Therapy. Methods & Clinical Development
|
January 24, 2020
7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy
Heather L Gray-Edwards, Anne S Maguire, Nouha Salibi, et al.
Annals of Neurology
|
August 1, 2023
Life-Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy
Aime K Johnson, Victoria J McCurdy, Heather L Gray-Edwards, et al.
The New England Journal of Medicine
|
February 10, 2026
AAV9 Gene Therapy in Type II GM1 Gangliosidosis - A Phase 1-2 Trial
Connor J Lewis, Precilla D'Souza, Jean M Johnston, et al.
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of 3
Search research articles
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Showing results (11-20 of 21) with videos related to
Sort By:
Page
of 3
Molecular Genetics and Metabolism
|
December 7, 2024
Clinical and biochemical abnormalities in a feline model of GM2 activator deficiency
Sidney J Beecy, Amanda L Gross, Anne S Maguire, et al.
Biorxiv : the Preprint Server for Biology
|
November 28, 2024
Intravenous gene therapy improves lifespan and clinical outcomes in feline Sandhoff Disease
Anne S Maguire, Linh Ta, Amanda L Gross, et al.
Molecular Therapy. Methods & Clinical Development
|
November 2, 2022
AAVrh10 vector corrects pathology in animal models of GM1 gangliosidosis and achieves widespread distribution in the CNS of nonhuman primates
Michaël Hocquemiller, Laura Giersch, Xin Mei, et al.
The International Journal of Neuropsychopharmacology
|
December 14, 2018
Positive N-Methyl-D-Aspartate Receptor Modulation by Rapastinel Promotes Rapid and Sustained Antidepressant-Like Effects
John E Donello, Pradeep Banerjee, Yong-Xin Li, et al.
Brain : a Journal of Neurology
|
August 19, 2021
Intravenous delivery of adeno-associated viral gene therapy in feline GM1 gangliosidosis
Amanda L Gross, Heather L Gray-Edwards, Cassie N Bebout, et al.
Ebiomedicine
|
June 2, 2023
A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosis
Pamela Kell, Rohini Sidhu, Mingxing Qian, et al.
Neuroscience
|
November 7, 2016
AAV-mediated gene delivery attenuates neuroinflammation in feline Sandhoff disease
Allison M Bradbury, Tiffany A Peterson, Amanda L Gross, et al.
Molecular Therapy. Methods & Clinical Development
|
January 24, 2020
7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy
Heather L Gray-Edwards, Anne S Maguire, Nouha Salibi, et al.
Annals of Neurology
|
August 1, 2023
Life-Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy
Aime K Johnson, Victoria J McCurdy, Heather L Gray-Edwards, et al.
The New England Journal of Medicine
|
February 10, 2026
AAV9 Gene Therapy in Type II GM1 Gangliosidosis - A Phase 1-2 Trial
Connor J Lewis, Precilla D'Souza, Jean M Johnston, et al.
Page
of 3