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The Journal of Gene Medicine|March 18, 2010
In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophyQingsong Wang, Haifang Yin, Patrizia Camelliti, et al.
Toxicological Sciences : an Official Journal of the Society of Toxicology|January 12, 2018
2'-O-(2-Methoxyethyl) Nucleosides Are Not Phosphorylated or Incorporated Into the Genome of Human Lymphoblastoid TK6 CellsAmer F Saleh, Martin Bachman, Catherine C Priestley, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 14, 2010
Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouseHaiFang Yin, Corinne Betts, Amer F Saleh, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 21, 2011
Pip5 transduction peptides direct high efficiency oligonucleotide-mediated dystrophin exon skipping in heart and phenotypic correction in mdx miceHaiFang Yin, Amer F Saleh, Corinne Betts, et al.
International Journal of Toxicology|March 5, 2025
An Industry Perspective on the Use of Novel Excipients in Lipid Nanoparticles-Nonclinical ConsiderationsLorrene A Buckley, Jessica E Sutherland, Prachi Borude, et al.
Small Science|January 14, 2026
Triplet RNA Lipid Nanoparticles for Locoregional Cancer ImmunotherapyAdam A Walters, Yue Qin, Amer F Saleh, et al.
Scientific Reports|November 24, 2015
Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomicsAnna M L Coenen-Stass, Graham McClorey, Raquel Manzano, et al.
Proceedings of the National Academy of Sciences of the United States of America|September 14, 2016
Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophySuzan M Hammond, Gareth Hazell, Fazel Shabanpoor, et al.
Nucleic Acid Therapeutics|January 17, 2015
Peptide nanoparticle delivery of charge-neutral splice-switching morpholino oligonucleotidesPeter Järver, Eman M Zaghloul, Andrey A Arzumanov, et al.
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