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Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 4, 2016
Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Maria Garcia-Gomez, Andrea Calabria, Maria Garcia-Bravo, et al.
The New England Journal of Medicine
|
July 16, 2011
MYO1E mutations and childhood familial focal segmental glomerulosclerosis
Caterina Mele, Paraskevas Iatropoulos, Roberta Donadelli, et al.
Cell Stem Cell
|
October 7, 2022
Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells
Samuele Ferrari, Aurelien Jacob, Daniela Cesana, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 3, 2020
Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
Raisa Jofra Hernández, Andrea Calabria, Francesca Sanvito, et al.
Genes
|
December 23, 2022
A Whole-Genome Sequencing Study Implicates GRAMD1B in Multiple Sclerosis Susceptibility
Federica Esposito, Ana Maria Osiceanu, Melissa Sorosina, et al.
The Journal of Clinical Investigation
|
August 12, 2020
Sleeping Beauty-engineered CAR T cells achieve antileukemic activity without severe toxicities
Chiara F Magnani, Giuseppe Gaipa, Federico Lussana, et al.
Nature
|
October 23, 2024
Long-term lineage commitment in haematopoietic stem cell gene therapy
Andrea Calabria, Giulio Spinozzi, Daniela Cesana, et al.
Lancet (London, England)
|
June 13, 2016
Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial
Maria Sessa, Laura Lorioli, Francesca Fumagalli, et al.
Blood
|
March 6, 2024
Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis
Pamela Quaranta, Luca Basso-Ricci, Raisa Jofra Hernandez, et al.
Nature Medicine
|
January 22, 2019
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia
Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese, et al.
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of 5
Search research articles
Search
Showing results (31-40 of 45) with videos related to
Sort By:
Page
of 5
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 4, 2016
Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Maria Garcia-Gomez, Andrea Calabria, Maria Garcia-Bravo, et al.
The New England Journal of Medicine
|
July 16, 2011
MYO1E mutations and childhood familial focal segmental glomerulosclerosis
Caterina Mele, Paraskevas Iatropoulos, Roberta Donadelli, et al.
Cell Stem Cell
|
October 7, 2022
Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells
Samuele Ferrari, Aurelien Jacob, Daniela Cesana, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 3, 2020
Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
Raisa Jofra Hernández, Andrea Calabria, Francesca Sanvito, et al.
Genes
|
December 23, 2022
A Whole-Genome Sequencing Study Implicates GRAMD1B in Multiple Sclerosis Susceptibility
Federica Esposito, Ana Maria Osiceanu, Melissa Sorosina, et al.
The Journal of Clinical Investigation
|
August 12, 2020
Sleeping Beauty-engineered CAR T cells achieve antileukemic activity without severe toxicities
Chiara F Magnani, Giuseppe Gaipa, Federico Lussana, et al.
Nature
|
October 23, 2024
Long-term lineage commitment in haematopoietic stem cell gene therapy
Andrea Calabria, Giulio Spinozzi, Daniela Cesana, et al.
Lancet (London, England)
|
June 13, 2016
Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial
Maria Sessa, Laura Lorioli, Francesca Fumagalli, et al.
Blood
|
March 6, 2024
Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis
Pamela Quaranta, Luca Basso-Ricci, Raisa Jofra Hernandez, et al.
Nature Medicine
|
January 22, 2019
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia
Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese, et al.
Page
of 5