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Frontiers in Cell and Developmental Biology
|
July 24, 2024
Single cell RNA sequencing of human FAPs reveals different functional stages in Duchenne muscular dystrophy
Esther Fernández-Simón, Patricia Piñol-Jurado, Rasya Gokul-Nath, et al.
The Lancet. Neurology
|
February 21, 2026
Safety and efficacy of fordadistrogene movaparvovec in ambulatory participants with Duchenne muscular dystrophy (CIFFREO): a phase 3, double-blind, randomised, placebo-controlled study
Francesco Muntoni, Andres Nascimento, Jinhong Shin, et al.
International Journal of Molecular Sciences
|
April 13, 2023
Innovative Computerized Dystrophin Quantification Method Based on Spectral Confocal Microscopy
Anna Codina, Mònica Roldán, Daniel Natera-de Benito, et al.
Frontiers in Aging Neuroscience
|
August 30, 2017
Differences in Adipose Tissue and Lean Mass Distribution in Patients with Collagen VI Related Myopathies Are Associated with Disease Severity and Physical Ability
M A Rodríguez, Luís M Del Rio Barquero, Carlos I Ortez, et al.
Journal of Neuromuscular Diseases
|
April 11, 2023
Full-Length SMN Transcript in Extracellular Vesicles as Biomarker in Individuals with Spinal Muscular Atrophy Type 2 Treated with Nusinersen
Selena Trifunov, Daniel Natera-de Benito, Laura Carrera-García, et al.
Annals of Clinical and Translational Neurology
|
May 30, 2025
Fetal Akinesia/Hypokinesia and Arthrogryposis of Neuromuscular Origin: Etiologic Groups, Genetics, and Phenotypic Spectrum
Florencia Pérez-Vidarte, Berta Estévez-Arias, Leslie Matalonga, et al.
Journal of Neurology
|
August 9, 2011
A retrospective clinical study of the treatment of slow-channel congenital myasthenic syndrome
Amina Chaouch, Juliane S Müller, Velina Guergueltcheva, et al.
Pediatric Neurology
|
April 24, 2021
Copper Toxicity Associated With an ATP7A-Related Complex Phenotype
Daniel Natera-de Benito, Abel Sola, Paulo Rego Sousa, et al.
Pediatric Neurology
|
December 17, 2020
The Phenotype and Genotype of Congenital Myopathies Based on a Large Pediatric Cohort
Daniel Natera-de Benito, Carlos Ortez, Cristina Jou, et al.
Frontiers in Neurology
|
August 6, 2024
Long-term efficacy, safety, and patient-reported outcomes of apitegromab in patients with spinal muscular atrophy: results from the 36-month TOPAZ study
Thomas O Crawford, John W Day, Darryl C De Vivo, et al.
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Search research articles
Search
Showing results (11-20 of 55) with videos related to
Sort By:
Page
of 6
Frontiers in Cell and Developmental Biology
|
July 24, 2024
Single cell RNA sequencing of human FAPs reveals different functional stages in Duchenne muscular dystrophy
Esther Fernández-Simón, Patricia Piñol-Jurado, Rasya Gokul-Nath, et al.
The Lancet. Neurology
|
February 21, 2026
Safety and efficacy of fordadistrogene movaparvovec in ambulatory participants with Duchenne muscular dystrophy (CIFFREO): a phase 3, double-blind, randomised, placebo-controlled study
Francesco Muntoni, Andres Nascimento, Jinhong Shin, et al.
International Journal of Molecular Sciences
|
April 13, 2023
Innovative Computerized Dystrophin Quantification Method Based on Spectral Confocal Microscopy
Anna Codina, Mònica Roldán, Daniel Natera-de Benito, et al.
Frontiers in Aging Neuroscience
|
August 30, 2017
Differences in Adipose Tissue and Lean Mass Distribution in Patients with Collagen VI Related Myopathies Are Associated with Disease Severity and Physical Ability
M A Rodríguez, Luís M Del Rio Barquero, Carlos I Ortez, et al.
Journal of Neuromuscular Diseases
|
April 11, 2023
Full-Length SMN Transcript in Extracellular Vesicles as Biomarker in Individuals with Spinal Muscular Atrophy Type 2 Treated with Nusinersen
Selena Trifunov, Daniel Natera-de Benito, Laura Carrera-García, et al.
Annals of Clinical and Translational Neurology
|
May 30, 2025
Fetal Akinesia/Hypokinesia and Arthrogryposis of Neuromuscular Origin: Etiologic Groups, Genetics, and Phenotypic Spectrum
Florencia Pérez-Vidarte, Berta Estévez-Arias, Leslie Matalonga, et al.
Journal of Neurology
|
August 9, 2011
A retrospective clinical study of the treatment of slow-channel congenital myasthenic syndrome
Amina Chaouch, Juliane S Müller, Velina Guergueltcheva, et al.
Pediatric Neurology
|
April 24, 2021
Copper Toxicity Associated With an ATP7A-Related Complex Phenotype
Daniel Natera-de Benito, Abel Sola, Paulo Rego Sousa, et al.
Pediatric Neurology
|
December 17, 2020
The Phenotype and Genotype of Congenital Myopathies Based on a Large Pediatric Cohort
Daniel Natera-de Benito, Carlos Ortez, Cristina Jou, et al.
Frontiers in Neurology
|
August 6, 2024
Long-term efficacy, safety, and patient-reported outcomes of apitegromab in patients with spinal muscular atrophy: results from the 36-month TOPAZ study
Thomas O Crawford, John W Day, Darryl C De Vivo, et al.
Page
of 6