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Journal of the Peripheral Nervous System : JPNS|April 13, 2022
Validation of the Italian version of the pediatric CMT quality of life outcome measureIsabella Moroni, Federica Rachele Danti, Davide Pareyson, et al.
Mitochondrion|April 2, 2021
SARS-CoV-2 infection in patients with primary mitochondrial diseases: Features and outcomes in ItalyMichelangelo Mancuso, Chiara La Morgia, Maria Lucia Valentino, et al.
Clinical Therapeutics|March 14, 2025
PHEMI-Phenylbutyrate in Patients With Lactic Acidosis: A Pilot, Single Arm, Phase I/II, Open-Label TrialSilvia Marchet, Alessia Catania, Anna Ardissone, et al.
Journal of Human Genetics|March 14, 2018
Compound heterozygous missense and deep intronic variants in NDUFAF6 unraveled by exome sequencing and mRNA analysisAlessia Catania, Anna Ardissone, Daniela Verrigni, et al.
Orphanet Journal of Rare Diseases|April 5, 2018
KARS-related diseases: progressive leukoencephalopathy with brainstem and spinal cord calcifications as new phenotype and a review of literatureAnna Ardissone, Davide Tonduti, Andrea Legati, et al.
Molecular Genetics and Metabolism|December 6, 2021
Alexander disease evolution over time: data from an Italian cohort of pediatric-onset patientsEleonora Mura, Francesco Nicita, Silvia Masnada, et al.
American Journal of Human Genetics|May 6, 2017
Mutations in Epigenetic Regulation Genes Are a Major Cause of Overgrowth with Intellectual DisabilityKatrina Tatton-Brown, Chey Loveday, Shawn Yost, et al.
European Journal of Neurology|June 7, 2021
A cross-sectional, prospective ocular motor study in 72 patients with Niemann-Pick disease type CTatiana Bremova-Ertl, Larry Abel, Mark Walterfang, et al.
Orphanet Journal of Rare Diseases|October 10, 2021
Clinical, imaging, biochemical and molecular features in Leigh syndrome: a study from the Italian network of mitochondrial diseasesAnna Ardissone, Claudio Bruno, Daria Diodato, et al.
Genes|July 29, 2023
NGS-Based Genetic Analysis in a Cohort of Italian Patients with Suspected Inherited Myopathies and/or HyperCKemiaFederica Invernizzi, Rossella Izzo, Isabel Colangelo, et al.
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