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Plos One|April 26, 2023
Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophyVandana Ayyar Gupta, Jacqueline M Pitchforth, Joana Domingos, et al.Journal of Neuromuscular Diseases|June 6, 2018
Evaluator Training and Reliability for SMA Global Nusinersen Trials1Allan M Glanzman, Elena S Mazzone, Sally Dunaway Young, et al.Neuromuscular Disorders : NMD|June 29, 2025
Levels of exercise exposure among people living with neuromuscular disorders: lessons learned from real-world dataMark Richardson, Virginie Kinet, Karen Wong, et al.Annals of Clinical and Translational Neurology|June 19, 2019
Natural history of limb girdle muscular dystrophy R9 over 6 years: searching for trial endpointsAlexander P Murphy, Jasper Morrow, Julia R Dahlqvist, et al.Plos One|August 23, 2013
Quantitative muscle MRI as an assessment tool for monitoring disease progression in LGMD2I: a multicentre longitudinal studyTracey A Willis, Kieren G Hollingsworth, Anna Coombs, et al.Plos One|March 4, 2014
Quantitative magnetic resonance imaging in limb-girdle muscular dystrophy 2I: a multinational cross-sectional studyTracey A Willis, Kieren G Hollingsworth, Anna Coombs, et al.Neurology. Genetics|July 13, 2023
Longitudinal Analysis of Respiratory Function of Different Types of Limb Girdle Muscular Dystrophies Reveals Independent TrajectoriesRobert Muni-Lofra, Eduard Juanola-Mayos, Marianela Schiava, et al.European Journal of Neurology|April 1, 2024
Functional abilities, respiratory and cardiac function in a large cohort of adults with Duchenne muscular dystrophy treated with glucocorticoidsMarianela Schiava, Robert Muni Lofra, John P Bourke, et al.Plos One|February 22, 2017
Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment toolDanielle Ramsey, Mariacristina Scoto, Anna Mayhew, et al.Muscle & Nerve|June 27, 2015
Old measures and new scores in spinal muscular atrophy patientsElena Mazzone, Jacqueline Montes, Marion Main, et al.Pageof 6