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Medrxiv : the Preprint Server for Health Sciences
|
January 10, 2024
Loss of Function of the Cytoplasmic Fe-S Assembly Protein CIAO1 Causes a Neuromuscular Disorder with Compromise of Nucleocytoplasmic Fe-S Enzymes
Nunziata Maio, Rotem Orbach, Irina Zaharieva, et al.
Annals of Clinical and Translational Neurology
|
July 23, 2022
GGPS1-associated muscular dystrophy with and without hearing loss
Rauan Kaiyrzhanov, Luke Perry, Clarissa Rocca, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
March 15, 2013
Titin founder mutation is a common cause of myofibrillar myopathy with early respiratory failure
Gerald Pfeffer, Rita Barresi, Ian J Wilson, et al.
The Journal of Clinical Investigation
|
July 1, 2024
CIAO1 loss of function causes a neuromuscular disorder with compromise of nucleocytoplasmic Fe-S enzymes
Nunziata Maio, Rotem Orbach, Irina T Zaharieva, et al.
Nature Genetics
|
December 5, 2006
Gain-of-function SOS1 mutations cause a distinctive form of Noonan syndrome
Marco Tartaglia, Len A Pennacchio, Chen Zhao, et al.
Annals of Clinical and Translational Neurology
|
May 15, 2026
Early Clinical, Imaging, and Pathological Characteristics of SRPK3/TTN-Digenic Myopathy
Rotem Orbach, Sandra Donkervoort, Carola Hedberg-Oldfors, et al.
Human Mutation
|
February 12, 2009
Germline BRAF mutations in Noonan, LEOPARD, and cardiofaciocutaneous syndromes: molecular diversity and associated phenotypic spectrum
Anna Sarkozy, Claudio Carta, Sonia Moretti, et al.
Human Mutation
|
January 25, 2022
Recessive variants in COL25A1 gene as novel cause of arthrogryposis multiplex congenita with ocular congenital cranial dysinnervation disorder
Daniel Natera-de Benito, Julie A Jurgens, Alison Yeung, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
November 24, 2025
The burden of TTN variants in the genomic era: analysis of 18,462 individuals from the Solve-RD consortium and general recommendations
Maria Francesca Di Feo, Ida Paramonov, Leslie Matalonga Borrel, et al.
Nature Genetics
|
August 18, 2009
Mutation of SHOC2 promotes aberrant protein N-myristoylation and causes Noonan-like syndrome with loose anagen hair
Viviana Cordeddu, Elia Di Schiavi, Len A Pennacchio, et al.
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of 14
Search research articles
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Showing results (101-110 of 137) with videos related to
Sort By:
Page
of 14
Medrxiv : the Preprint Server for Health Sciences
|
January 10, 2024
Loss of Function of the Cytoplasmic Fe-S Assembly Protein CIAO1 Causes a Neuromuscular Disorder with Compromise of Nucleocytoplasmic Fe-S Enzymes
Nunziata Maio, Rotem Orbach, Irina Zaharieva, et al.
Annals of Clinical and Translational Neurology
|
July 23, 2022
GGPS1-associated muscular dystrophy with and without hearing loss
Rauan Kaiyrzhanov, Luke Perry, Clarissa Rocca, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
March 15, 2013
Titin founder mutation is a common cause of myofibrillar myopathy with early respiratory failure
Gerald Pfeffer, Rita Barresi, Ian J Wilson, et al.
The Journal of Clinical Investigation
|
July 1, 2024
CIAO1 loss of function causes a neuromuscular disorder with compromise of nucleocytoplasmic Fe-S enzymes
Nunziata Maio, Rotem Orbach, Irina T Zaharieva, et al.
Nature Genetics
|
December 5, 2006
Gain-of-function SOS1 mutations cause a distinctive form of Noonan syndrome
Marco Tartaglia, Len A Pennacchio, Chen Zhao, et al.
Annals of Clinical and Translational Neurology
|
May 15, 2026
Early Clinical, Imaging, and Pathological Characteristics of SRPK3/TTN-Digenic Myopathy
Rotem Orbach, Sandra Donkervoort, Carola Hedberg-Oldfors, et al.
Human Mutation
|
February 12, 2009
Germline BRAF mutations in Noonan, LEOPARD, and cardiofaciocutaneous syndromes: molecular diversity and associated phenotypic spectrum
Anna Sarkozy, Claudio Carta, Sonia Moretti, et al.
Human Mutation
|
January 25, 2022
Recessive variants in COL25A1 gene as novel cause of arthrogryposis multiplex congenita with ocular congenital cranial dysinnervation disorder
Daniel Natera-de Benito, Julie A Jurgens, Alison Yeung, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
November 24, 2025
The burden of TTN variants in the genomic era: analysis of 18,462 individuals from the Solve-RD consortium and general recommendations
Maria Francesca Di Feo, Ida Paramonov, Leslie Matalonga Borrel, et al.
Nature Genetics
|
August 18, 2009
Mutation of SHOC2 promotes aberrant protein N-myristoylation and causes Noonan-like syndrome with loose anagen hair
Viviana Cordeddu, Elia Di Schiavi, Len A Pennacchio, et al.
Page
of 14