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Cell Stem Cell|February 7, 2025
Two is better than one: Advancing gene therapy protocols for enhanced safety and efficacyGiulia Hardouin, Annarita Miccio
Methods in Molecular Biology (Clifton, N.J.)|November 9, 2020
A Genome Editing System for Therapeutical Targeting of Stem CellsGiacomo Frati, Annarita Miccio
Progress in Molecular Biology and Translational Science|June 27, 2021
Genome editing approaches to β-hemoglobinopathiesMégane Brusson, Annarita Miccio
Journal of Clinical Medicine|February 2, 2021
Genome Editing for β-Hemoglobinopathies: Advances and ChallengesGiacomo Frati, Annarita Miccio
Cell Stem Cell|April 5, 2024
The difficult translational pathway from animal models to patientsMarina Cavazzana, Annarita Miccio
IUBMB Life|October 2, 2019
GATA factor transcriptional activity: Insights from genome-wide binding profilesOriana Romano, Annarita Miccio
Medecine Sciences : M/S|January 31, 2025
[A CRISPR/Cas approach to β-haemoglobinopathies]Megane Brusson, Annarita Miccio
Molecular and Cellular Biology|May 5, 2010
Role of the GATA-1/FOG-1/NuRD pathway in the expression of human beta-like globin genesAnnarita Miccio, Gerd A Blobel
Frontiers in Genome Editing|October 29, 2021
Base and Prime Editing Technologies for Blood DisordersPanagiotis Antoniou, Annarita Miccio, Mégane Brusson
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 6, 2017
Gene Therapy for β-HemoglobinopathiesMarina Cavazzana, Chiara Antoniani, Annarita Miccio
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