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Journal of Biopharmaceutical Statistics
|
April 12, 2025
The role of regulatory flexibility in the review and approval process of rare disease drug development
Shein-Chung Chow, Anne Pariser, Steven Galson
Journal of Biopharmaceutical Statistics
|
April 12, 2025
Use of alternative and confirmatory data in support of rare disease drug development
Shein-Chung Chow, Anne Pariser, Steven Galson
Clinical Cancer Research : an Official Journal of the American Association for Cancer Research
|
June 22, 2012
Rare cancer trial design: lessons from FDA approvals
Himabindu Gaddipati, Ke Liu, Anne Pariser, et al.
Science Translational Medicine
|
December 24, 2010
Training the translational scientist
Rebecca D Jackson, Sherine Gabriel, Anne Pariser, et al.
Methods of Information in Medicine
|
November 4, 2020
Leveraging the UMLS As a Data Standard for Rare Disease Data Normalization and Harmonization
Qian Zhu, Dac-Trung Nguyen, Eric Sid, et al.
Pharmaceutical Medicine
|
July 8, 2024
Increasing Diversity, Equity, Inclusion, and Accessibility in Rare Disease Clinical Trials
Gareth Baynam, Simeón Baker, Charles Steward, et al.
Orphanet Journal of Rare Diseases
|
April 13, 2022
The national economic burden of rare disease in the United States in 2019
Grace Yang, Inna Cintina, Anne Pariser, et al.
Journal of Biomedical Semantics
|
November 13, 2020
An integrative knowledge graph for rare diseases, derived from the Genetic and Rare Diseases Information Center (GARD)
Qian Zhu, Dac-Trung Nguyen, Ivan Grishagin, et al.
JMIR Medical Informatics
|
October 2, 2020
Phenotypically Similar Rare Disease Identification from an Integrative Knowledge Graph for Data Harmonization: Preliminary Study
Qian Zhu, Dac-Trung Nguyen, Gioconda Alyea, et al.
Nature Biotechnology
|
August 9, 2008
Neutralizing antibodies to therapeutic enzymes: considerations for testing, prevention and treatment
Jinhai Wang, Jay Lozier, Gibbes Johnson, et al.
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of 2
Search research articles
Search
Showing results (1-10 of 16) with videos related to
Sort By:
Page
of 2
Journal of Biopharmaceutical Statistics
|
April 12, 2025
The role of regulatory flexibility in the review and approval process of rare disease drug development
Shein-Chung Chow, Anne Pariser, Steven Galson
Journal of Biopharmaceutical Statistics
|
April 12, 2025
Use of alternative and confirmatory data in support of rare disease drug development
Shein-Chung Chow, Anne Pariser, Steven Galson
Clinical Cancer Research : an Official Journal of the American Association for Cancer Research
|
June 22, 2012
Rare cancer trial design: lessons from FDA approvals
Himabindu Gaddipati, Ke Liu, Anne Pariser, et al.
Science Translational Medicine
|
December 24, 2010
Training the translational scientist
Rebecca D Jackson, Sherine Gabriel, Anne Pariser, et al.
Methods of Information in Medicine
|
November 4, 2020
Leveraging the UMLS As a Data Standard for Rare Disease Data Normalization and Harmonization
Qian Zhu, Dac-Trung Nguyen, Eric Sid, et al.
Pharmaceutical Medicine
|
July 8, 2024
Increasing Diversity, Equity, Inclusion, and Accessibility in Rare Disease Clinical Trials
Gareth Baynam, Simeón Baker, Charles Steward, et al.
Orphanet Journal of Rare Diseases
|
April 13, 2022
The national economic burden of rare disease in the United States in 2019
Grace Yang, Inna Cintina, Anne Pariser, et al.
Journal of Biomedical Semantics
|
November 13, 2020
An integrative knowledge graph for rare diseases, derived from the Genetic and Rare Diseases Information Center (GARD)
Qian Zhu, Dac-Trung Nguyen, Ivan Grishagin, et al.
JMIR Medical Informatics
|
October 2, 2020
Phenotypically Similar Rare Disease Identification from an Integrative Knowledge Graph for Data Harmonization: Preliminary Study
Qian Zhu, Dac-Trung Nguyen, Gioconda Alyea, et al.
Nature Biotechnology
|
August 9, 2008
Neutralizing antibodies to therapeutic enzymes: considerations for testing, prevention and treatment
Jinhai Wang, Jay Lozier, Gibbes Johnson, et al.
Page
of 2