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Expert Opinion on Biological Therapy|June 26, 2018
Progress in gene and cell therapies for the neuronal ceroid lipofuscinosesAnthony Donsante, Nicholas M BoulisExpert Review of Neurotherapeutics|October 16, 2023
Current and emerging targeted therapies for spinal muscular atrophyYuliya Lakhina, Nicholas M Boulis, Anthony DonsanteMethods in Molecular Biology (Clifton, N.J.)|November 28, 2015
Gene Therapy for the Treatment of Neurological Disorders: Amyotrophic Lateral SclerosisZachary T McEachin, Anthony Donsante, Nicholas BoulisMolecular Therapy. Nucleic Acids|June 27, 2013
Fetal Brain-directed AAV Gene Therapy Results in Rapid, Robust, and Persistent Transduction of Mouse Choroid Plexus EpitheliaMarie Reine Haddad, Anthony Donsante, Patricia Zerfas, et al.Annals of Neurology|February 6, 2009
Translational read-through of a nonsense mutation in ATP7A impacts treatment outcome in Menkes diseaseStephen G Kaler, Jingrong Tang, Anthony Donsante, et al.Journal of Visualized Experiments : Jove|April 15, 2024
Intrathecal Vector Delivery in Juvenile Rats via Lumbar Cistern InjectionAnthony Donsante, Shauna A Rasmussen, Judith L Fridovich-KeilAmerican Journal of Medical Genetics. Part A|August 28, 2010
Somatic mosaicism in Menkes disease suggests choroid plexus-mediated copper transport to the developing brainAnthony Donsante, Paul Johnson, Laura A Jansen, et al.Molecular Diagnosis & Therapy|July 31, 2025
The Future of Chemogenetics for the Treatment of SpasticityKelly Poth, Roy Raheb Khelo, Anthony Donsante, et al.Molecular Genetics and Metabolism|August 30, 2008
Clinical outcomes in Menkes disease patients with a copper-responsive ATP7A mutation, G727RJingrong Tang, Anthony Donsante, Vishal Desai, et al.Frontiers in Molecular Neuroscience|August 30, 2016
Gene, Stem Cell, and Alternative Therapies for SCA 1Jacob L Wagner, Deirdre M O'Connor, Anthony Donsante, et al.Pageof 3