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Plos Genetics|October 21, 2020
Evaluation of both exonic and intronic variants for effects on RNA splicing allows for accurate assessment of the effectiveness of precision therapiesAnya T Joynt, Taylor A Evans, Matthew J Pellicore, et al.American Journal of Respiratory and Critical Care Medicine|March 20, 2019
Correlating Cystic Fibrosis Transmembrane Conductance Regulator Function with Clinical Features to Inform Precision Treatment of Cystic FibrosisAllison F McCague, Karen S Raraigh, Matthew J Pellicore, et al.Plos Genetics|November 17, 2018
Capitalizing on the heterogeneous effects of CFTR nonsense and frameshift variants to inform therapeutic strategy for cystic fibrosisNeeraj Sharma, Taylor A Evans, Matthew J Pellicore, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|March 12, 2026
SORT LNPs encapsulating Cas9 mRNA achieve efficient editing in skeletal muscle in a dystrophic mouse modelSukanya Iyer, Katelyn Daman, Yehui Sun, et al.Nature Biotechnology|September 25, 2024
Increasing intracellular dNTP levels improves prime editing efficiencyPengpeng Liu, Karthikeyan Ponnienselvan, Thomas Nyalile, et al.Pageof 2