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American Journal of Hematology
|
March 25, 2015
Velaglucerase alfa (VPRIV) enzyme replacement therapy in patients with Gaucher disease: Long-term data from phase III clinical trials
Derralynn A Hughes, Derlis E Gonzalez, Elena A Lukina, et al.
Plos One
|
November 27, 2013
Glucosylsphingosine is a highly sensitive and specific biomarker for primary diagnostic and follow-up monitoring in Gaucher disease in a non-Jewish, Caucasian cohort of Gaucher disease patients
Arndt Rolfs, Anne-Katrin Giese, Ulrike Grittner, et al.
Skeletal Radiology
|
May 13, 2014
Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat
Ravi S Kamath, Elena Lukina, Nora Watman, et al.
British Journal of Haematology
|
May 30, 2012
Characteristics of type I Gaucher disease associated with persistent thrombocytopenia after treatment with imiglucerase for 4-5 years
Carla E M Hollak, Nadia Belmatoug, J Alexander Cole, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 23, 2009
A validated disease severity scoring system for adults with type 1 Gaucher disease
Neal J Weinreb, Maria D Cappellini, Timothy M Cox, et al.
International Journal of Molecular Sciences
|
July 13, 2024
<i>GBA1</i>-Associated Parkinson's Disease Is a Distinct Entity
Aliaksandr Skrahin, Mia Horowitz, Majdolen Istaiti, et al.
American Journal of Hematology
|
May 14, 2016
Long-term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment-naïve patients with Gaucher disease
Ari Zimran, Gloria Durán, Atul Mehta, et al.
JAMA Neurology
|
April 24, 2014
Comparison of Parkinson risk in Ashkenazi Jewish patients with Gaucher disease and GBA heterozygotes
Roy N Alcalay, Tama Dinur, Timothy Quinn, et al.
Archives of Internal Medicine
|
February 13, 2008
Prevalence of type 1 Gaucher disease in the United States
Neal J Weinreb, Hans C Andersson, Maryam Banikazemi, et al.
Orphanet Journal of Rare Diseases
|
January 7, 2022
Development and validation of Gaucher disease type 1 (GD1)-specific patient-reported outcome measures (PROMs) for clinical monitoring and for clinical trials
Deborah Elstein, Nadia Belmatoug, Patrick Deegan, et al.
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of 24
Search research articles
Search
Showing results (211-220 of 238) with videos related to
Sort By:
Page
of 24
American Journal of Hematology
|
March 25, 2015
Velaglucerase alfa (VPRIV) enzyme replacement therapy in patients with Gaucher disease: Long-term data from phase III clinical trials
Derralynn A Hughes, Derlis E Gonzalez, Elena A Lukina, et al.
Plos One
|
November 27, 2013
Glucosylsphingosine is a highly sensitive and specific biomarker for primary diagnostic and follow-up monitoring in Gaucher disease in a non-Jewish, Caucasian cohort of Gaucher disease patients
Arndt Rolfs, Anne-Katrin Giese, Ulrike Grittner, et al.
Skeletal Radiology
|
May 13, 2014
Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat
Ravi S Kamath, Elena Lukina, Nora Watman, et al.
British Journal of Haematology
|
May 30, 2012
Characteristics of type I Gaucher disease associated with persistent thrombocytopenia after treatment with imiglucerase for 4-5 years
Carla E M Hollak, Nadia Belmatoug, J Alexander Cole, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 23, 2009
A validated disease severity scoring system for adults with type 1 Gaucher disease
Neal J Weinreb, Maria D Cappellini, Timothy M Cox, et al.
International Journal of Molecular Sciences
|
July 13, 2024
<i>GBA1</i>-Associated Parkinson's Disease Is a Distinct Entity
Aliaksandr Skrahin, Mia Horowitz, Majdolen Istaiti, et al.
American Journal of Hematology
|
May 14, 2016
Long-term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment-naïve patients with Gaucher disease
Ari Zimran, Gloria Durán, Atul Mehta, et al.
JAMA Neurology
|
April 24, 2014
Comparison of Parkinson risk in Ashkenazi Jewish patients with Gaucher disease and GBA heterozygotes
Roy N Alcalay, Tama Dinur, Timothy Quinn, et al.
Archives of Internal Medicine
|
February 13, 2008
Prevalence of type 1 Gaucher disease in the United States
Neal J Weinreb, Hans C Andersson, Maryam Banikazemi, et al.
Orphanet Journal of Rare Diseases
|
January 7, 2022
Development and validation of Gaucher disease type 1 (GD1)-specific patient-reported outcome measures (PROMs) for clinical monitoring and for clinical trials
Deborah Elstein, Nadia Belmatoug, Patrick Deegan, et al.
Page
of 24