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Molecular Therapy. Nucleic Acids|September 14, 2016
Reprogramming the Dynamin 2 mRNA by Spliceosome-mediated RNA Trans-splicingDelphine Trochet, Bernard Prudhon, Arnaud Jollet, et al.Drug Delivery|March 2, 2005
New synthetic glycolipids for targeted gene transfer: synthesis, formulation in lipoplexes and specific interaction with lectinMarie Carrière, Virginie Escriou, Arnaud Jollet, et al.Nature Structural & Molecular Biology|December 28, 2010
Selective silencing of mutated mRNAs in DM1 by using modified hU7-snRNAsVirginie François, Arnaud F Klein, Cyriaque Beley, et al.Nucleic Acids Research|July 18, 2013
Dystrophin rescue by trans-splicing: a strategy for DMD genotypes not eligible for exon skipping approachesStéphanie Lorain, Cécile Peccate, Maëva Le Hir, et al.Molecular Therapy. Nucleic Acids|March 4, 2018
Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular DystrophyFeriel Azibani, Astrid Brull, Ludovic Arandel, et al.Disease Models & Mechanisms|February 12, 2017
Immortalized human myotonic dystrophy muscle cell lines to assess therapeutic compoundsLudovic Arandel, Micaela Polay Espinoza, Magdalena Matloka, et al.Nature Communications|May 29, 2015
Abnormal splicing switch of DMD's penultimate exon compromises muscle fibre maintenance in myotonic dystrophyFrédérique Rau, Jeanne Lainé, Laetitita Ramanoudjame, et al.The Journal of Allergy and Clinical Immunology|December 17, 2013
Recombination-activating gene 1 (Rag1)-deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndromeNiek P van Til, Roya Sarwari, Trudi P Visser, et al.Nature Communications|April 12, 2016
Splicing misregulation of SCN5A contributes to cardiac-conduction delay and heart arrhythmia in myotonic dystrophyFernande Freyermuth, Frédérique Rau, Yosuke Kokunai, et al.Pageof 1