Showing results (11-20 of 36) with videos related to

Sort By:
Pageof 4
Annals of Neurology|September 7, 2023
Hurler Syndrome Glycosaminoglycans Decrease in Cerebrospinal Fluid without Brain-Targeted TherapyTroy C Lund, Elizabeth Braunlin, Lynda E Polgreen, et al.
Frontiers in Pediatrics|August 5, 2021
A Guidance for Concomitant Drug Reconciliation Prior to Allogeneic Hematopoietic Cell Transplantation in Children and Young AdultsBeth Apsel Winger, Susie E Long, Jordan Brooks, et al.
F&S Reports|March 24, 2023
A case series of adrenoleukodystrophy in children conceived through in vitro fertilization with an egg donorCrystal Chang, Ashish O Gupta, Paul J Orchard, et al.
Journal of the Endocrine Society|April 22, 2022
Primary Adrenal Insufficiency in a Boy with Type I Diabetes: The Importance of Considering X-linked AdrenoleukodystrophyRebecca E Wiersma, Ashish O Gupta, Troy C Lund, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 13, 2026
Promoting donor microglial replacement through augmented conditioning or radiation sensitivityTroy C Lund, Willa Durose, Emma Schindhelm, et al.
Molecular Therapy. Advances|May 15, 2026
CSF GAG non-reducing ends in MPS IH after peripheral and brain-penetrating therapies: A model comparing IV non-targeted ERT and HCTTroy C Lund, John E Wagner, Susie Long, et al.
Journal of Neurosurgery. Pediatrics|March 15, 2024
Natural history of craniovertebral abnormalities in a single-center study in 54 patients with Hurler syndromeShiwei Huang, David R Nascene, Ryan Shanley, et al.
Expert Opinion on Biological Therapy|September 15, 2022
Treatment of cerebral adrenoleukodystrophy: allogeneic transplantation and lentiviral gene therapyAshish O Gupta, Gerald Raymond, Elizabeth I Pierpont, et al.
Transplantation and Cellular Therapy|February 6, 2025
Bodyweight and Absolute Lymphocyte Count-Based Dosing of Rabbit Anti-thymocyte Globulin Results in Early CD4+ Immune Reconstitution in Patients with Inborn Errors of Metabolism Undergoing Umbilical Cord Blood TransplantationDaniel Drozdov, Jessica Kandil, Susie E Long, et al.
Transplantation and Cellular Therapy|December 9, 2021
Busulfan dose Recommendation in Inherited Metabolic Disorders: Population Pharmacokinetic AnalysisTakuto Takahashi, Sílvia M Illamola, Cathryn A Jennissen, et al.
Pageof 4