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Journal of Inherited Metabolic Disease|September 9, 2021
Differential outcomes for frontal versus posterior demyelination in childhood cerebral adrenoleukodystrophyAshish O Gupta, David R Nascene, Ryan Shanley, et al.Journal of Neurosurgery. Pediatrics|May 9, 2025
Longitudinal clinical and imaging analysis of hydrocephalus in a single-center study in 57 patients with mucopolysaccharidosis type IH (Hurler syndrome)Shiwei Huang, David R Nascene, Ryan Shanley, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|August 7, 2024
Secondary failure of lentiviral vector gene therapy in a cerebral adrenoleukodystrophy patient with an ABCD1 whole-gene deletionTroy C Lund, Paul J Orchard, David R Nascene, et al.Brain : a Journal of Neurology|September 24, 2025
Neurofilament light chain as a prognostic marker in cerebral adrenoleukodystrophyElizabeth I Pierpont, Ashish O Gupta, Julie B Eisengart, et al.Bone Marrow Transplantation|January 14, 2021
Consensus opinion on immune-mediated cytopenias after hematopoietic cell transplant for inherited metabolic disordersAshish O Gupta, Jaap Jan Boelens, Christen L Ebens, et al.Journal of Neuroimmunology|June 19, 2024
Targeting VEGF-mediated blood-brain barrier disruption in advanced cerebral leukodystrophyAshish O Gupta, Justin W Furcich, David R Nascene, et al.Scientific Reports|May 14, 2022
Glycoprotein nonmetastatic melanoma protein B (GNMPB) as a novel biomarker for cerebral adrenoleukodystrophyLeyla A Taghizadeh, Carina J King, David R Nascene, et al.Neurology|July 4, 2020
Neurocognitive benchmarks following transplant for emerging cerebral adrenoleukodystrophyElizabeth I Pierpont, David R Nascene, Ryan Shanley, et al.Stem Cells (Dayton, Ohio)|July 29, 2025
Loss of peroxisome function promotes oxidative stress induced hematopoiesisEmma A Schindhelm, Amada Blake, Megan M Constans, et al.Cytotherapy|July 6, 2024
International Society for Cell & Gene Therapy Stem Cell Engineering Committee report on the current state of hematopoietic stem and progenitor cell-based genomic therapies and the challenges facedAshish O Gupta, Melissa Azul, Senthil Velan Bhoopalan, et al.Pageof 4