Search research articles
Contact Us
Filters
Showing results (11-20 of 122) with videos related to
Page
of 13
Sort By:
Pediatrics
|
February 6, 2008
Successful management of difficult infusion-associated reactions in a young patient with mucopolysaccharidosis type VI receiving recombinant human arylsulfatase B (galsulfase [Naglazyme])
Katherine H Kim, Celeste Decker, Barbara K Burton
Molecular Genetics and Metabolism Reports
|
June 27, 2017
Successful reduction of high-sustained anti-idursulfase antibody titers by immune modulation therapy in a patient with severe mucopolysaccharidosis type II
Katherine H Kim, Yoav H Messinger, Barbara K Burton
Molecular Genetics and Metabolism
|
July 13, 2013
High dose genistein aglycone therapy is safe in patients with mucopolysaccharidoses involving the central nervous system
Katherine H Kim, Charlotte Dodsworth, Andrea Paras, et al.
Journal of Inherited Metabolic Disease
|
September 10, 2017
Survival in idursulfase-treated and untreated patients with mucopolysaccharidosis type II: data from the Hunter Outcome Survey (HOS)
Barbara K Burton, Virginie Jego, Jaromir Mikl, et al.
Molecular Genetics and Metabolism
|
May 12, 2009
Home infusion therapy is safe and enhances compliance in patients with mucopolysaccharidoses
Barbara K Burton, Chani Wiesman, Andrea Paras, et al.
Molecular Genetics and Metabolism
|
July 20, 2010
Sapropterin therapy increases stability of blood phenylalanine levels in patients with BH4-responsive phenylketonuria (PKU)
Barbara K Burton, Heather Bausell, Rachel Katz, et al.
Molecular Genetics and Metabolism
|
November 20, 2025
Evaluation and follow-up of newborns screening positive for mucopolysaccharidosis II: Results from an international modified Delphi consensus
Barbara K Burton, N Matthew Ellinwood, Katey K Hoffman, et al.
Acta Paediatrica (Oslo, Norway : 1992)
|
January 23, 2013
Mucopolysaccharidosis type III (Sanfilippo syndrome) and misdiagnosis of idiopathic developmental delay, attention deficit/hyperactivity disorder or autism spectrum disorder
Frits A Wijburg, Grzegorz Węgrzyn, Barbara K Burton, et al.
Pediatrics
|
November 23, 2017
The Initial Evaluation of Patients After Positive Newborn Screening: Recommended Algorithms Leading to a Confirmed Diagnosis of Pompe Disease
Barbara K Burton, David F Kronn, Wuh-Liang Hwu, et al.
Molecular Genetics and Metabolism Reports
|
September 1, 2022
Pegvaliase dose escalation to 80 mg daily may lead to efficacy in patients who do not exhibit an optimal response at lower doses
Erika R Vucko, Kirsten E Havens, Joshua J Baker, et al.
Page
of 13
Search research articles
Search
Showing results (11-20 of 122) with videos related to
Sort By:
Page
of 13
Pediatrics
|
February 6, 2008
Successful management of difficult infusion-associated reactions in a young patient with mucopolysaccharidosis type VI receiving recombinant human arylsulfatase B (galsulfase [Naglazyme])
Katherine H Kim, Celeste Decker, Barbara K Burton
Molecular Genetics and Metabolism Reports
|
June 27, 2017
Successful reduction of high-sustained anti-idursulfase antibody titers by immune modulation therapy in a patient with severe mucopolysaccharidosis type II
Katherine H Kim, Yoav H Messinger, Barbara K Burton
Molecular Genetics and Metabolism
|
July 13, 2013
High dose genistein aglycone therapy is safe in patients with mucopolysaccharidoses involving the central nervous system
Katherine H Kim, Charlotte Dodsworth, Andrea Paras, et al.
Journal of Inherited Metabolic Disease
|
September 10, 2017
Survival in idursulfase-treated and untreated patients with mucopolysaccharidosis type II: data from the Hunter Outcome Survey (HOS)
Barbara K Burton, Virginie Jego, Jaromir Mikl, et al.
Molecular Genetics and Metabolism
|
May 12, 2009
Home infusion therapy is safe and enhances compliance in patients with mucopolysaccharidoses
Barbara K Burton, Chani Wiesman, Andrea Paras, et al.
Molecular Genetics and Metabolism
|
July 20, 2010
Sapropterin therapy increases stability of blood phenylalanine levels in patients with BH4-responsive phenylketonuria (PKU)
Barbara K Burton, Heather Bausell, Rachel Katz, et al.
Molecular Genetics and Metabolism
|
November 20, 2025
Evaluation and follow-up of newborns screening positive for mucopolysaccharidosis II: Results from an international modified Delphi consensus
Barbara K Burton, N Matthew Ellinwood, Katey K Hoffman, et al.
Acta Paediatrica (Oslo, Norway : 1992)
|
January 23, 2013
Mucopolysaccharidosis type III (Sanfilippo syndrome) and misdiagnosis of idiopathic developmental delay, attention deficit/hyperactivity disorder or autism spectrum disorder
Frits A Wijburg, Grzegorz Węgrzyn, Barbara K Burton, et al.
Pediatrics
|
November 23, 2017
The Initial Evaluation of Patients After Positive Newborn Screening: Recommended Algorithms Leading to a Confirmed Diagnosis of Pompe Disease
Barbara K Burton, David F Kronn, Wuh-Liang Hwu, et al.
Molecular Genetics and Metabolism Reports
|
September 1, 2022
Pegvaliase dose escalation to 80 mg daily may lead to efficacy in patients who do not exhibit an optimal response at lower doses
Erika R Vucko, Kirsten E Havens, Joshua J Baker, et al.
Page
of 13