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Journal of Medicinal Chemistry|April 18, 2003
Tripeptide probes for tripeptidyl protease I production via gene transferMeeKyoung Kim, Qinwen Mao, Beverly L Davidson, et al.
Trends in Neurosciences|July 5, 2011
Clarifying lysosomal storage diseasesMark L Schultz, Luis Tecedor, Michael Chang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 8, 2023
Targeted long-read sequencing captures CRISPR editing and AAV integration outcomes in brainBryan P Simpson, Carolyn M Yrigollen, Aleksandar Izda, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 17, 2012
Sialic acid deposition impairs the utility of AAV9, but not peptide-modified AAVs for brain gene therapy in a mouse model of lysosomal storage diseaseYong Hong Chen, Kristin Claflin, James C Geoghegan, et al.
The Journal of Neuroscience : the Official Journal of the Society for Neuroscience|November 11, 2005
Silencing primary dystonia: lentiviral-mediated RNA interference therapy for DYT1 dystoniaPedro Gonzalez-Alegre, Nicole Bode, Beverly L Davidson, et al.
Plos One|June 16, 2012
MiR-34a represses Numbl in murine neural progenitor cells and antagonizes neuronal differentiationSarah K Fineberg, Poppy Datta, Colleen S Stein, et al.
Neurobiology of Disease|September 30, 2010
A knock-in reporter mouse model for Batten disease reveals predominant expression of Cln3 in visual, limbic and subcortical motor structuresSong-Lin Ding, Luis Tecedor, Colleen S Stein, et al.
Experimental Neurology|December 4, 2002
Widespread dispersal of cholera toxin subunit b to brain and spinal cord neurons following systemic deliveryJoseph M Alisky, Christopher I van de Wetering, Beverly L Davidson
Annals of Neurology|August 29, 2025
Co-Opting MBNL-Dependent Alternative Splicing Cassette Exons to Control Gene Therapy in Myotonic DystrophySamuel T Carrell, Ellie M Carrell, Ryan Giovenco, et al.
Brain : a Journal of Neurology|October 23, 2015
Broad distribution of ataxin 1 silencing in rhesus cerebella for spinocerebellar ataxia type 1 therapyMegan S Keiser, Jeffrey H Kordower, Pedro Gonzalez-Alegre, et al.
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